(Q34956532)

English

Efficacy of sapropterin dihydrochloride in increasing phenylalanine tolerance in children with phenylketonuria: a phase III, randomized, double-blind, placebo-controlled study

scientific article

Statements

Efficacy of sapropterin dihydrochloride in increasing phenylalanine tolerance in children with phenylketonuria: a phase III, randomized, double-blind, placebo-controlled study (English)
Friedrich K Trefz
Barbara K Burton
Nicola Longo
Mercedes Martinez-Pardo Casanova
Daniel J Gruskin
Alex Dorenbaum
Emil D Kakkis
Eric A Crombez
Paul Harmatz
Mark H Lipson
Andrzej Milanowski
Linda Marie Randolph
Chester B Whitley
Jon A Wolff
Judith Bebchuk
Heidi Christ-Schmidt
Julia B Hennermann
Sapropterin Study Group

Identifiers

 
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