(Q34956532)
Statements
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Efficacy of sapropterin dihydrochloride in increasing phenylalanine tolerance in children with phenylketonuria: a phase III, randomized, double-blind, placebo-controlled study (English)
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Dorothy K Grange
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Friedrich K Trefz
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Barbara K Burton
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Nicola Longo
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Mercedes Martinez-Pardo Casanova
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Daniel J Gruskin
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Alex Dorenbaum
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Emil D Kakkis
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Eric A Crombez
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Paul Harmatz
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Mark H Lipson
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Andrzej Milanowski
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Linda Marie Randolph
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Chester B Whitley
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Jon A Wolff
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Judith Bebchuk
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Heidi Christ-Schmidt
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Julia B Hennermann
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Sapropterin Study Group
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Identifiers
1 reference