(Q37690306)

English

Efficacy, safety and population pharmacokinetics of sapropterin in PKU patients <4 years: results from the SPARK open-label, multicentre, randomized phase IIIb trial

scientific article published on 09 March 2017

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scholarly article

1 reference

Europe PubMed Central

22 August 2017

Efficacy, safety and population pharmacokinetics of sapropterin in PKU patients <4 years: results from the SPARK open-label, multicentre, randomized phase IIIb trial (English)

1 reference

Europe PubMed Central

22 August 2017

multicenter clinical trial

0 references

1 reference

based on heuristic

inferred from title

author name string

Ania C Muntau

1

1 reference

Europe PubMed Central

22 August 2017

Alberto Burlina

2

1 reference

Europe PubMed Central

22 August 2017

François Eyskens

3

1 reference

Europe PubMed Central

22 August 2017

Peter Freisinger

4

1 reference

Europe PubMed Central

22 August 2017

Corinne De Laet

5

1 reference

Europe PubMed Central

22 August 2017

Vincenzo Leuzzi

6

1 reference

Europe PubMed Central

22 August 2017

Frank Rutsch

7

1 reference

Europe PubMed Central

22 August 2017

H Serap Sivri

8

1 reference

Europe PubMed Central

22 August 2017

Suresh Vijay

9

1 reference

Europe PubMed Central

22 August 2017

Milva Orquidea Bal

10

1 reference

Europe PubMed Central

22 August 2017

Gwendolyn Gramer

11

1 reference

Europe PubMed Central

22 August 2017

Renata Pazdírková

12

1 reference

Europe PubMed Central

22 August 2017

Maureen Cleary

13

1 reference

Europe PubMed Central

22 August 2017

Amelie S Lotz-Havla

14

1 reference

Europe PubMed Central

22 August 2017

Alain Munafo

15

1 reference

Europe PubMed Central

22 August 2017

Diane R Mould

16

1 reference

Europe PubMed Central

22 August 2017

Flavie Moreau-Stucker

17

1 reference

Europe PubMed Central

22 August 2017

Daniela Rogoff

18

1 reference

Europe PubMed Central

22 August 2017

publication date

9 March 2017

1 reference

Europe PubMed Central

22 August 2017

Orphanet Journal of Rare Diseases

1 reference

Europe PubMed Central

22 August 2017

12

1 reference

Europe PubMed Central

22 August 2017

47

1 reference

Europe PubMed Central

22 August 2017

1

1 reference

Europe PubMed Central

22 August 2017

https://scigraph.springernature.com/pub.10.1186/s13023-017-0600-x

0 references

A prospective population pharmacokinetic analysis of sapropterin dihydrochloride in infants and young children with phenylketonuria

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5343543

23 August 2017

Phenylketonuria: nutritional advances and challenges

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5343543

23 August 2017

Reassessment of phenylalanine tolerance in adults with phenylketonuria is needed as body mass changes

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5343543

23 August 2017

Sapropterin: a review of its use in the treatment of primary hyperphenylalaninaemia

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5343543

23 August 2017

Efficacy of sapropterin dihydrochloride in increasing phenylalanine tolerance in children with phenylketonuria: a phase III, randomized, double-blind, placebo-controlled study

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5343543

23 August 2017

Vancomycin pharmacokinetics in preterm neonates and the prediction of adult clearance

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5343543

23 August 2017

Phenylketonuria: tyrosine supplementation in phenylalanine-restricted diets

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5343543

23 August 2017

Intelligence and quality of dietary treatment in phenylketonuria

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5343543

23 August 2017

Key European guidelines for the diagnosis and management of patients with phenylketonuria.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5343543

6 September 2017

Sapropterin dihydrochloride for the treatment of hyperphenylalaninemias

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5343543

6 September 2017

Diagnosis, classification, and genetics of phenylketonuria and tetrahydrobiopterin (BH4) deficiencies.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5343543

6 September 2017

Pharmacokinetics of sapropterin in patients with phenylketonuria

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5343543

23 June 2018

Maturation and growth of renal function: dosing renally cleared drugs in children

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5343543

23 June 2018

Long-term developmental progression in infants and young children taking sapropterin for phenylketonuria: a two-year analysis of safety and efficacy.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5343543

1 September 2018

Phenylketonuria Scientific Review Conference: state of the science and future research needs

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5343543

1 September 2018

Simultaneous determination of phenylalanine and tyrosine in peripheral capillary blood by HPLC with ultraviolet detection.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5343543

1 September 2018

Effect of BH(4) supplementation on phenylalanine tolerance

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5343543

1 September 2018

Blood phenylalanine monitoring for dietary compliance among patients with phenylketonuria: comparison of methods.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5343543

1 September 2018

Management of phenylketonuria and hyperphenylalaninemia: the French guidelines

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5343543

1 September 2018

Normal clinical outcome in untreated subjects with mild hyperphenylalaninemia

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5343543

1 September 2018

International database of tetrahydrobiopterin deficiencies

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=5343543

1 September 2018

Sapropterin is safe and effective in patients less than 4-years-old with BH4-responsive phenylalanine hydrolase deficiency

1 reference

https://pubmed.ncbi.nlm.nih.gov/28274234

12 December 2020

based on heuristic

inferred from PubMed ID database lookup

Some Considerations on the Design of Population Pharmacokinetic Studies

1 reference

https://pubmed.ncbi.nlm.nih.gov/28274234

12 December 2020

based on heuristic

inferred from PubMed ID database lookup

Comparison of tandem mass spectrometry and amino acid analyzer for phenylalanine and tyrosine monitoring--implications for clinical management of patients with hyperphenylalaninemia

1 reference

https://pubmed.ncbi.nlm.nih.gov/28274234

12 December 2020

based on heuristic

inferred from PubMed ID database lookup

Phenylketonuria

1 reference

https://pubmed.ncbi.nlm.nih.gov/28274234

12 December 2020

based on heuristic

inferred from PubMed ID database lookup

Recommendations on the dietary management of phenylketonuria. Report of Medical Research Council Working Party on Phenylketonuria

1 reference

https://pubmed.ncbi.nlm.nih.gov/28274234

12 December 2020

based on heuristic

inferred from PubMed ID database lookup

Management of phenylketonuria and hyperphenylalaninemia

1 reference

https://pubmed.ncbi.nlm.nih.gov/28274234

12 December 2020

based on heuristic

inferred from PubMed ID database lookup

Identifiers

10.1186/S13023-017-0600-X

1 reference

Europe PubMed Central

22 August 2017

Dimensions Publication ID

0 references

1 reference

Europe PubMed Central

22 August 2017

1 reference

Europe PubMed Central

22 August 2017

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