(Q37695619)

22 August 2017

Bioluminescent imaging of a marking transgene and correction of Fabry mice by neonatal injection of recombinant lentiviral vectors (English)

1 reference

22 August 2017

0 references

Makoto Yoshimitsu

1

1 reference

22 August 2017

Takeya Sato

2

1 reference

22 August 2017

Kesheng Tao

3

1 reference

22 August 2017

Jagdeep S Walia

4

1 reference

22 August 2017

Vanessa I Rasaiah

5

1 reference

22 August 2017

Gillian T Sleep

6

1 reference

22 August 2017

Gary J Murray

7

1 reference

22 August 2017

Armando G Poeppl

8

1 reference

22 August 2017

John Underwood

9

1 reference

22 August 2017

Lori West

10

1 reference

22 August 2017

Roscoe O Brady

11

1 reference

22 August 2017

Jeffrey A Medin

12

1 reference

22 August 2017

language of work or name

English

0 references

publication date

18 November 2004

1 reference

22 August 2017

6

1 reference

Proceedings of the National Academy of Sciences of the United States of America

inferred from page(s)

published in

1 reference

22 August 2017

101

1 reference

22 August 2017

16909-16914

1 reference

22 August 2017

48

1 reference

Therapeutic neonatal hepatic gene therapy in mucopolysaccharidosis VII dogs

22 August 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=534735

Advances in in vivo bioluminescence imaging of gene expression

23 August 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=534735

Germline transmission and tissue-specific expression of transgenes delivered by lentiviral vectors

23 August 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=534735

Enzyme replacement therapy in Fabry disease: a randomized controlled trial

23 August 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=534735

Preselective gene therapy for Fabry disease

23 August 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=534735

Adeno-associated viral vector-mediated gene transfer results in long-term enzymatic and functional correction in multiple organs of Fabry mice

23 August 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=534735

Long-term enzyme correction and lipid reduction in multiple organs of primary and secondary transplanted Fabry mice receiving transduced bone marrow cells

23 August 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=534735

Aging accentuates and bone marrow transplantation ameliorates metabolic defects in Fabry disease mice

23 August 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=534735

Neonatal gene transfer leads to widespread correction of pathology in a murine model of lysosomal storage disease.

23 August 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=534735

alpha-Galactosidase A deficient mice: a model of Fabry disease

23 August 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=534735

Correction in trans for Fabry disease: expression, secretion and uptake of alpha-galactosidase A in patient-derived cells driven by a high-titer recombinant retroviral vector

23 August 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=534735

In vivo gene delivery and stable transduction of nondividing cells by a lentiviral vector

23 August 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=534735

Affinity purification of alpha-galactosidase A from human spleen, placenta, and plasma with elimination of pyrogen contamination. Properties of the purified splenic enzyme compared to other forms

23 August 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=534735

Use of the human elongation factor 1 alpha promoter as a versatile and efficient expression system

23 August 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=534735

Improvement of skeletal lesions in mice with mucopolysaccharidosis type vii by neonatal adenoviral gene transfer

23 August 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=534735

Evaluation of pathological manifestations of disease in mucopolysaccharidosis VII mice after neonatal hepatic gene therapy.

14 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=534735

Safety and efficacy of recombinant human alpha-galactosidase A replacement therapy in Fabry's disease

14 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=534735

Systematic determination of the packaging limit of lentiviral vectors

14 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=534735

Circulating alpha-galactosidase A derived from transduced bone marrow cells: relevance for corrective gene transfer for Fabry disease.

28 September 2017

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0407572101

Noninvasive optical imaging of firefly luciferase reporter gene expression in skeletal muscles of living mice

21 January 2018

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0407572101

Gene transfer by lentiviral vectors is limited by nuclear translocation and rescued by HIV-1 pol sequences

21 January 2018

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0407572101

Efficacy and safety analyses of a recombinant human immunodeficiency virus type 1 derived vector system

21 January 2018

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0407572101

Reversal of pathology in the entire brain of mucopolysaccharidosis type VII mice after lentivirus-mediated gene transfer.

21 January 2018

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0407572101

Transduction of hepatocytes after neonatal delivery of a Moloney murine leukemia virus based retroviral vector results in long-term expression of beta-glucuronidase in mucopolysaccharidosis VII dogs

21 January 2018

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0407572101

Enzymatic Defect in Fabry's Disease

21 January 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/15550536

12 December 2020

inferred from PubMed ID database lookup

Immunologic tolerance

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/15550536

12 December 2020

inferred from PubMed ID database lookup

Percutaneous intravenous injection in neonatal mice

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/15550536

12 December 2020

inferred from PubMed ID database lookup

Identifiers

DOI

10.1073/PNAS.0407572101

1 reference

22 August 2017

0 references

1 reference

22 August 2017

1 reference