(Q43976641)

28 November 2017

Immune reconstitution in ADA-SCID after PBL gene therapy and discontinuation of enzyme replacement (English)

1 reference

28 November 2017

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4

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28 November 2017

Francesca Ficara

5

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Alessandra Mortellaro

Alessandra Mortellaro

3

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Alessandro Aiuti

Alessandro Aiuti

1

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Maria Grazia Roncarolo

Maria Grazia Roncarolo

12

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Claudio Bordignon

13

Claudio Bordignon

1 reference

28 November 2017

10

Hans D Ochs

1 reference

28 November 2017

11

Luigi D Notarangelo

1 reference

28 November 2017

Sergio Vai

2

1 reference

28 November 2017

Grazia Andolfi

6

1 reference

28 November 2017

Giuliana Ferrari

7

1 reference

28 November 2017

Antonella Tabucchi

8

1 reference

28 November 2017

Filippo Carlucci

9

1 reference

28 November 2017

language of work or name

English

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publication date

1 May 2002

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28 November 2017

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28 November 2017

8

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28 November 2017

423-425

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28 November 2017

5

1 reference

https://scigraph.springernature.com/pub.10.1038/nm0502-423

28 November 2017

0 references

cites work

Gene therapy in peripheral blood lymphocytes and bone marrow for ADA- immunodeficient patients

1 reference

https://api.crossref.org/works/10.1038%2FNM0502-423

T lymphocyte-directed gene therapy for ADA- SCID: initial trial results after 4 years.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FNM0502-423

Engraftment of gene-modified umbilical cord blood cells in neonates with adenosine deaminase deficiency

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FNM0502-423

Severe Combined Immunodeficiency and Adenosine Deaminase Deficiency

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FNM0502-423

Bone marrow transplantation only partially restores purine metabolites to normal in adenosine deaminase-deficient patients

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FNM0502-423

T lymphocytes with a normal ADA gene accumulate after transplantation of transduced autologous umbilical cord blood CD34+ cells in ADA-deficient SCID neonates.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FNM0502-423

Adenosine deaminase deficiency: genotype-phenotype correlations based on expressed activity of 29 mutant alleles

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FNM0502-423

Transfer of the ADA gene into bone marrow cells and peripheral blood lymphocytes for the treatment of patients affected by ADA-deficient SCID.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FNM0502-423

21 January 2018

Identifiers

DOI

10.1038/NM0502-423

1 reference

28 November 2017

1 reference