(Q62822383)
Statements
GEMINI (English)
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An Open-Label Safety Study of Retinal Gene Therapy for Choroideremia With Bilateral, Sequential Administration of Adeno-Associated Viral Vector (AAV2) Encoding Rab Escort Protein 1 (REP1) (English)
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6 November 2017
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31 March 2020
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15
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18 year
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