(Q63397869)

English

Pre-Symptomatic Study of Intravenous AVXS-101 in Spinal Muscular Atrophy (SMA) for Patients With Multiple Copies of SMN2

clinical trial

Statements

SPR1NT (English)
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A Global Study of a Single, One-Time Dose of AVXS-101 Delivered to Infants With Genetically Diagnosed and Pre-symptomatic Spinal Muscular Atrophy With Multiple Copies of SMN2 (English)
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10 April 2018
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October 2020
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27
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Identifiers

 
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