(Q63593973)
Statements
A Randomized, Placebo-Controlled, Crossover Study to Evaluate the Safety and Efficacy of Amifampridine Phosphate in Ambulatory Patients With Spinal Muscular Atrophy (SMA) Type 3 (English)
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21 January 2019
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15 December 2019
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12
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6 year
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50 year
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