(Q63401760)
Statements
MODIFY (English)
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A Multicenter, dOuble-blind, ranDomized, Placebo-controlled, Parallel-group Study to Determine the effIcacy and Safety of Lucerastat Oral Monotherapy in Adult Subjects With FabrY Disease (English)
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21 June 2018
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7 December 2019
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108
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18 year
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