(Q24802168)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:15109394%20AND%20SRC:MED&resulttype=core&format=json

27 December 2019

title

Recombinant adeno-associated virus type 2-mediated gene delivery into the Rpe65-/- knockout mouse eye results in limited rescue (English)

1 reference

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27 December 2019

0 references

0 references

4

1 reference

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27 December 2019

T. Michael Redmond

6

1 reference

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27 December 2019

author name string

Chooi-May Lai

1

1 reference

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27 December 2019

Meaghan JT Yu

2

1 reference

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27 December 2019

Meliha Brankov

3

1 reference

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27 December 2019

Xiaohuai Zhou

5

1 reference

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27 December 2019

P Elizabeth Rakoczy

8

1 reference

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27 December 2019

Kristina Narfstrom

7

1 reference

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27 December 2019

publication date

27 April 2004

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:15109394%20AND%20SRC:MED&resulttype=core&format=json

Genetic Vaccines and Therapy

27 December 2019

published in

1 reference

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27 December 2019

volume

2

1 reference

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27 December 2019

issue

1

1 reference

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27 December 2019

page(s)

3

1 reference

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https://scigraph.springernature.com/pub.10.1186/1479-0556-2-3

27 December 2019

exact match

1 reference

9 September 2019

https://scigraph.springernature.com/pub.10.1186/1479-0556-2-3

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Recombinant adeno-associated virus serotype 4 mediates unique and exclusive long-term transduction of retinal pigmented epithelium in rat, dog, and nonhuman primate after subretinal delivery

28 September 2017

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28 September 2017

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28 September 2017

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28 September 2017

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Cross-packaging of a single adeno-associated virus (AAV) type 2 vector genome into multiple AAV serotypes enables transduction with broad specificity

28 September 2017

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28 September 2017

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AAV-mediated delivery of ciliary neurotrophic factor prolongs photoreceptor survival in the rhodopsin knockout mouse

28 September 2017

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28 September 2017

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Rapid restoration of visual pigment and function with oral retinoid in a mouse model of childhood blindness

28 September 2017

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Kinetics of recombinant adeno-associated virus-mediated gene transfer

28 September 2017

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Molecular mechanism for silencing virally transduced genes involves histone deacetylation and chromatin condensation

28 September 2017

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Leber congenital amaurosis

28 September 2017

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Stable transgene expression in rod photoreceptors after recombinant adeno-associated virus-mediated gene transfer to monkey retina

28 September 2017

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Retinal dystrophy of Swedish briard/briard-beagle dogs is due to a 4-bp deletion in RPE65.

28 September 2017

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Congenital stationary night blindness in the dog: common mutation in the RPE65 gene indicates founder effect.

28 September 2017

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28 September 2017

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28 September 2017

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28 September 2017

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28 September 2017

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30 May 2018

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30 May 2018

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28 November 2018

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28 November 2018

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28 November 2018

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28 November 2018

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28 November 2018

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28 November 2018

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11-cis-retinal reduces constitutive opsin phosphorylation and improves quantum catch in retinoid-deficient mouse rod photoreceptors

28 November 2018

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Kinetics of transgene expression in mouse retina following sub-retinal injection of recombinant adeno-associated virus

28 November 2018

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28 November 2018

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28 November 2018

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New views on RPE65 deficiency: the rod system is the source of vision in a mouse model of Leber congenital amaurosis.

28 November 2018

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Gene therapy restores vision in a canine model of childhood blindness

28 November 2018

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Transcriptionally active drugs improve adenovirus vector performance in vitro and in vivo

28 November 2018

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Recombinant adeno-associated virus purification using novel methods improves infectious titer and yield

28 November 2018

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Evaluation of adeno-associated virus-mediated gene transfer into the rat retina by clinical fluorescence photography

28 November 2018

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Rpe65 is necessary for production of 11-cis-vitamin A in the retinal visual cycle.

28 November 2018

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28 November 2018

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Slowly progressive changes of the retina and retinal pigment epithelium in Briard dogs with hereditary retinal dystrophy. A morphological study

28 November 2018

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12 December 2020

Early-onset severe rod-cone dystrophy in young children with RPE65 mutations

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12 December 2020

Mutational analysis and clinical correlation in Leber congenital amaurosis

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12 December 2020

Genetic analysis of RPE65: from human disease to mouse model

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12 December 2020

Identifiers

DOI

10.1186/1479-0556-2-3

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:15109394%20AND%20SRC:MED&resulttype=core&format=json

Dimensions Publication ID

27 December 2019

1 reference

9 September 2019

https://scigraph.springernature.com/pub.10.1186/1479-0556-2-3

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:15109394%20AND%20SRC:MED&resulttype=core&format=json

27 December 2019

1 reference