(Q28144597)

2

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Y P Tsao

3

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A Sakamoto

4

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E P Hoffman

5

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X Xiao

The cryptic life style of adeno-associated virus

6

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language of work or name

English

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publication date

January 1999

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published in

Gene Therapy

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volume

6

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page(s)

74-82

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issue

1

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cites work

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

Viral gene delivery to skeletal muscle: insights on maturation-dependent loss of fiber infectivity for adenovirus and herpes simplex type 1 viral vectors

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

Recombinant adeno-associated virus for muscle directed gene therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

Gene delivery to skeletal muscle results in sustained expression and systemic delivery of a therapeutic protein

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

Stable gene transfer and expression of human blood coagulation factor IX after intramuscular injection of recombinant adeno-associated virus

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

Direct intramuscular injection with recombinant AAV vectors results in sustained expression in a dog model of hemophilia

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

Long-term correction of obesity and diabetes in genetically obese mice by a single intramuscular injection of recombinant adeno-associated virus encoding mouse leptin

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

Adeno-associated virus-mediated delivery of erythropoietin leads to sustained elevation of hematocrit in nonhuman primates

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

From dystrophinopathy to sarcoglycanopathy: evolution of a concept of muscular dystrophy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

Mutations in the delta-sarcoglycan gene are a rare cause of autosomal recessive limb-girdle muscular dystrophy (LGMD2)

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

Mutations in the sarcoglycan genes in patients with myopathy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

Beta-sarcoglycan (A3b) mutations cause autosomal recessive muscular dystrophy with loss of the sarcoglycan complex

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

Genomic screening for beta-sarcoglycan gene mutations: missense mutations may cause severe limb-girdle muscular dystrophy type 2E (LGMD 2E)

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

Autosomal recessive limb-girdle muscular dystrophy, LGMD2F, is caused by a mutation in the delta-sarcoglycan gene

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

Beta-sarcoglycan: characterization and role in limb-girdle muscular dystrophy linked to 4q12

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

Characterization of delta-sarcoglycan, a novel component of the oligomeric sarcoglycan complex involved in limb-girdle muscular dystrophy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

A biochemical, genetic, and clinical survey of autosomal recessive limb girdle muscular dystrophies in Turkey

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

Genetic epidemiology of muscular dystrophies resulting from sarcoglycan gene mutations.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

Mutations in the dystrophin-associated protein gamma-sarcoglycan in chromosome 13 muscular dystrophy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

Deficiency of the 50K dystrophin-associated glycoprotein in severe childhood autosomal recessive muscular dystrophy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

Identification of the Syrian hamster cardiomyopathy gene.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

Both hypertrophic and dilated cardiomyopathies are caused by mutation of the same gene, delta-sarcoglycan, in hamster: an animal model of disrupted dystrophin-associated glycoprotein complex

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

Mutational diversity and hot spots in the alpha-sarcoglycan gene in autosomal recessive muscular dystrophy (LGMD2D)

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

epsilon-Sarcoglycan, a broadly expressed homologue of the gene mutated in limb-girdle muscular dystrophy 2D

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

Human epsilon-sarcoglycan is highly related to alpha-sarcoglycan (adhalin), the limb girdle muscular dystrophy 2D gene

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

Efficient and stable adeno-associated virus-mediated transduction in the skeletal muscle of adult immunocompetent mice

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

Induction of cellular DNA synthesis by purified adenovirus E1A proteins

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

Long-term gene expression and phenotypic correction using adeno-associated virus vectors in the mammalian brain

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

Long-term gene transfer in porcine myocardium after coronary infusion of an adeno-associated virus vector

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

Functional rescue of the sarcoglycan complex in the BIO 14.6 hamster using delta-sarcoglycan gene transfer.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

Dystrophin: the protein product of the Duchenne muscular dystrophy locus

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

Complete cloning of the duchenne muscular dystrophy (DMD) cDNA and preliminary genomic organization of the DMD gene in normal and affected individuals

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

The muscle creatine kinase gene is regulated by multiple upstream elements, including a muscle-specific enhancer

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

The basal lamina is a physical barrier to herpes simplex virus-mediated gene delivery to mature muscle fibers.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

7 January 2021

Efficient long-term gene transfer into muscle tissue of immunocompetent mice by adeno-associated virus vector

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

7 January 2021

Recombinant adeno-associated viral vectors mediate long-term transgene expression in muscle

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

7 January 2021

HyperCKemic, proximal muscular dystrophies and the dystrophin membrane cytoskeleton, including dystrophinopathies, sarcoglycanopathies, and merosinopathies.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

7 January 2021

Autosomal recessive muscular dystrophy and mutations of the sarcoglycan complex

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

7 January 2021

Selective defect of sarcoglycan complex in severe childhood autosomal recessive muscular dystrophy muscle

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

7 January 2021

Transduction of dendritic cells by DNA viral vectors directs the immune response to transgene products in muscle fibers

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

7 January 2021

A "humanized" green fluorescent protein cDNA adapted for high-level expression in mammalian cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

7 January 2021

Role for highly regulated rep gene expression in adeno-associated virus vector production

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3300830

7 January 2021