(Q30559496)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23817205%20AND%20SRC:MED&resulttype=core&format=json

4 March 2020

title

A single intravenous rAAV injection as late as P20 achieves efficacious and sustained CNS Gene therapy in Canavan mice (English)

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23817205%20AND%20SRC:MED&resulttype=core&format=json

4 March 2020

0 references

14

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23817205%20AND%20SRC:MED&resulttype=core&format=json

4 March 2020

Daniel A Kirschner

13

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23817205%20AND%20SRC:MED&resulttype=core&format=json

4 March 2020

author name string

Seemin Seher Ahmed

1

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23817205%20AND%20SRC:MED&resulttype=core&format=json

4 March 2020

Huapeng Li

2

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23817205%20AND%20SRC:MED&resulttype=core&format=json

4 March 2020

Chunyan Cao

3

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23817205%20AND%20SRC:MED&resulttype=core&format=json

4 March 2020

Elif M Sikoglu

4

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23817205%20AND%20SRC:MED&resulttype=core&format=json

4 March 2020

Andrew R Denninger

5

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23817205%20AND%20SRC:MED&resulttype=core&format=json

4 March 2020

Qin Su

6

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23817205%20AND%20SRC:MED&resulttype=core&format=json

4 March 2020

Samuel Eaton

7

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23817205%20AND%20SRC:MED&resulttype=core&format=json

4 March 2020

Ana A Liso Navarro

8

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23817205%20AND%20SRC:MED&resulttype=core&format=json

4 March 2020

Jun Xie

9

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23817205%20AND%20SRC:MED&resulttype=core&format=json

4 March 2020

Sylvia Szucs

10

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23817205%20AND%20SRC:MED&resulttype=core&format=json

4 March 2020

Hongwei Zhang

11

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23817205%20AND%20SRC:MED&resulttype=core&format=json

4 March 2020

Constance Moore

12

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23817205%20AND%20SRC:MED&resulttype=core&format=json

4 March 2020

Terence R Flotte

15

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23817205%20AND%20SRC:MED&resulttype=core&format=json

4 March 2020

Reuben Matalon

16

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23817205%20AND%20SRC:MED&resulttype=core&format=json

4 March 2020

Guangping Gao

17

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23817205%20AND%20SRC:MED&resulttype=core&format=json

4 March 2020

publication date

2 July 2013

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23817205%20AND%20SRC:MED&resulttype=core&format=json

4 March 2020

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23817205%20AND%20SRC:MED&resulttype=core&format=json

4 March 2020

volume

21

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23817205%20AND%20SRC:MED&resulttype=core&format=json

4 March 2020

issue

12

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23817205%20AND%20SRC:MED&resulttype=core&format=json

4 March 2020

page(s)

2136-2147

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23817205%20AND%20SRC:MED&resulttype=core&format=json

describes a project that uses

4 March 2020

ImageJ

1 reference

11 June 2022

https://www.ebi.ac.uk/europepmc/webservices/rest/PMC3863789/fullTextXML

inferred from PubMed Central ID database lookup

cites work

Global CNS gene delivery and evasion of anti-AAV-neutralizing antibodies by intrathecal AAV administration in non-human primates

1 reference

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Long-term follow-up after gene therapy for canavan disease.

20 June 2018

1 reference

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20 June 2018

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Aspartoacylase-lacZ knockin mice: an engineered model of Canavan disease

20 June 2018

1 reference

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Several rAAV vectors efficiently cross the blood-brain barrier and transduce neurons and astrocytes in the neonatal mouse central nervous system

20 June 2018

1 reference

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20 June 2018

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MicroRNA-regulated, systemically delivered rAAV9: a step closer to CNS-restricted transgene expression

20 June 2018

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RETRACTED ARTICLE: Rescue of the spinal muscular atrophy phenotype in a mouse model by early postnatal delivery of SMN

20 June 2018

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Molecular analysis of vector genome structures after liver transduction by conventional and self-complementary adeno-associated viral serotype vectors in murine and nonhuman primate models

20 June 2018

1 reference

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What is the optimal value of the g-ratio for myelinated fibers in the rat CNS? A theoretical approach

20 June 2018

1 reference

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Internodal myelination during development quantitated using X-ray diffraction.

20 June 2018

1 reference

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Comparative analysis of brain lipids in mice, cats, and humans with Sandhoff disease

20 June 2018

1 reference

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Nur7 is a nonsense mutation in the mouse aspartoacylase gene that causes spongy degeneration of the CNS

20 June 2018

1 reference

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Myelin lipid abnormalities in the aspartoacylase-deficient tremor rat.

20 June 2018

1 reference

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20 June 2018

1 reference

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20 June 2018

1 reference

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Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy

20 June 2018

1 reference

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Clinical protocol. Gene therapy of Canavan disease: AAV-2 vector for neurosurgical delivery of aspartoacylase gene (ASPA) to the human brain

20 June 2018

1 reference

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Functions of N-acetyl-L-aspartate and N-acetyl-L-aspartylglutamate in the vertebrate brain: role in glial cell-specific signaling

20 June 2018

1 reference

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Knock-out mouse for Canavan disease: a model for gene transfer to the central nervous system

20 June 2018

1 reference

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Spongy degeneration of the brain, Canavan disease: biochemical and molecular findings

20 June 2018

1 reference

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20 June 2018

1 reference

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Canavan disease. Analysis of the nature of the metabolic lesions responsible for development of the observed clinical symptoms

20 June 2018

1 reference

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20 June 2018

1 reference

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Cloning of the human aspartoacylase cDNA and a common missense mutation in Canavan disease

20 June 2018

1 reference

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20 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3863789

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20 June 2018

1 reference

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20 June 2018

1 reference

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Aspartoacylase deficiency and N-acetylaspartic aciduria in patients with canavan disease

20 June 2018

1 reference

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20 June 2018

1 reference

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Intravascular AAV9 preferentially targets neonatal neurons and adult astrocytes

20 June 2018

1 reference

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Structure and stability of internodal myelin in mouse models of hereditary neuropathy.

26 November 2018

1 reference

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High cholesterol level is essential for myelin membrane growth

26 November 2018

1 reference

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26 November 2018

1 reference

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26 November 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3863789

Aspartoacylase is restricted primarily to myelin synthesizing cells in the CNS: therapeutic implications for Canavan disease

26 November 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3863789

Neuronal pathology in the wobbler mouse brain revealed by in vivo proton magnetic resonance spectroscopy and immunocytochemistry

26 November 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3863789

Amidohydrolases of brain; enzymatic hydrolysis of N-acetyl-L-aspartate and other N-acyl-L-amino acids

26 November 2018

1 reference

12 December 2020

Purification, characterization, and localization of aspartoacylase from bovine brain

1 reference

12 December 2020

[Effect of hepatitis B virus X gene on the expression of spastic paraplegia 21]

1 reference

12 December 2020

Accumulation of N-acetyl-L-aspartate in the brain of the tremor rat, a mutant exhibiting absence-like seizure and spongiform degeneration in the central nervous system

1 reference

12 December 2020

Dopamine-beta-hydroxylase activity in human cerebrospinal fluid

1 reference

Crossref

https://api.crossref.org/works/10.1038%2FMT.2013.138

7 January 2021

inferred from DOI database lookup

Identifiers

DOI

10.1038/MT.2013.138

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23817205%20AND%20SRC:MED&resulttype=core&format=json

release_ewmdp5q4wncepnmk435jsbjgsy

4 March 2020

Fatcat ID

1 reference

Fatcat

https://api.fatcat.wiki/v0/release/ewmdp5q4wncepnmk435jsbjgsy

24 November 2022

mapped directly with Wikidata item

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23817205%20AND%20SRC:MED&resulttype=core&format=json

4 March 2020

PubMed publication ID

23817205

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23817205%20AND%20SRC:MED&resulttype=core&format=json