(Q33568987)

28 July 2017

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title

Alglucerase. A pharmacoeconomic appraisal of its use in the treatment of Gaucher's disease (English)

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28 July 2017

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R Whittington

1

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28 July 2017

K L Goa

series ordinal

2

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28 July 2017

language of work or name

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1 January 1995

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28 July 2017

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28 July 2017

volume

7

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28 July 2017

issue

1

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28 July 2017

page(s)

63-90

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Gaucher's disease: a pilot study of the symptomatic responses to enzyme replacement therapy

28 July 2017

cites work

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12 December 2020

Gaucher disease (type III): intellectual profile

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12 December 2020

Regression of bone lesions in Gaucher's disease during treatment with aminohydroxypropylidene bisphosphonate

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12 December 2020

Treatment of Gaucher's disease

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12 December 2020

Phenotype/genotype correlations in Gaucher disease type I: clinical and therapeutic implications.

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12 December 2020

Identification of Gaucher disease carriers: glucocerebrosidase antigen and DNA analysis

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12 December 2020

A 27-year experience with splenectomy for Gaucher's disease

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12 December 2020

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12 December 2020

An improved procedure for diagnosis of Gaucher disease using cultured skin fibroblasts and the chromogenic substrate, 2-hexadecanoylamino-4-nitrophenyl-beta-D-glucopyranoside

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12 December 2020

Partial splenectomy in Gaucher's disease: follow-up report

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12 December 2020

Clinical and biochemical outcome of marrow transplantation for Gaucher disease of the Norrbottnian type

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12 December 2020

The Organization and Delivery of Clinical Genetics Services

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12 December 2020

Orthotopic liver transplantation for type 1 Gaucher's disease

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12 December 2020

A double-blind study of 250 cases comparing cemented with cementless total hip arthroplasty. Cost-effectiveness and its impact on health-related quality of life.

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12 December 2020

Gaucher's disease: a disease with chronic stimulation of the immune system

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12 December 2020

Enzyme replacement therapy for Gaucher disease: critical investigations beyond demonstration of clinical efficacy

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12 December 2020

Dose-dependent responses to macrophage-targeted glucocerebrosidase in a child with Gaucher disease

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12 December 2020

Assay of glucocerebrosidase using a fluorescent analogue of glucocerebroside for the diagnosis of Gaucher disease

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12 December 2020

A procedure for the rapid purification in high yield of human glucocerebrosidase using immunoaffinity chromatography with monoclonal antibodies

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12 December 2020

Gaucher disease mutations in non-Jewish patients

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12 December 2020

Chimerism after liver transplantation for type IV glycogen storage disease and type 1 Gaucher's disease

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12 December 2020

Bone marrow transplantation in Europe--can the geographical differences be explained?

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12 December 2020

Cost-effectiveness of splenectomy versus intravenous gamma globulin in treatment of chronic immune thrombocytopenic purpura in childhood

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12 December 2020

Clinical decision making: from theory to practice. Rationing resources while improving quality. How to get more for less

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12 December 2020

Marked elevation of plasma chitotriosidase activity. A novel hallmark of Gaucher disease

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12 December 2020

Synthesis of a fluorescent derivative of glucosyl ceramide for the sensitive determination of glucocerebrosidase activity

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12 December 2020

Treatment of Gaucher's disease

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12 December 2020

Bone-marrow transplantation in severe Gaucher's disease

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12 December 2020

Renal transplantation in Type II Gaucher disease

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12 December 2020

Replacement therapy for inherited enzyme deficiency--macrophage-targeted glucocerebrosidase for Gaucher's disease

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12 December 2020

Gaucher disease: gene frequencies in the Ashkenazi Jewish population

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12 December 2020

Activator protein deficient Gaucher's disease. A second patient with the newly identified lipid storage disorder

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12 December 2020

Can we afford medical advances?

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12 December 2020

Ten years' experience of bone marrow transplantation for Gaucher disease.

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12 December 2020

Non-existence of a tight association between a 444leucine to proline mutation and phenotypes of Gaucher disease: high frequency of a NciI polymorphism in the non-neuronopathic form

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12 December 2020

A less costly regimen of alglucerase to treat Gaucher's disease.

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12 December 2020

Isolated horizontal supranuclear gaze palsy as a marker of severe systemic involvement in Gaucher's disease.

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12 December 2020

Creating the costliest orphan. The Orphan Drug Act in the development of Ceredase

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12 December 2020

Mutation analysis of 28 Gaucher disease patients: the Australasian experience

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12 December 2020

Misuse of marrow examination in the diagnosis of Gaucher disease

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12 December 2020

DNA mutational analysis of type 1 and type 3 Gaucher patients: how well do mutations predict phenotype?

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12 December 2020

Loosening of a noncemented porous-coated anatomic femoral component in Gaucher's disease. A case report and review of literature

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12 December 2020

[3 cases of Gaucher's disease (adult type), with reference to cases reported in Japan (1970-1981)]

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12 December 2020

Aminohydroxy propylidene bisphosphonate (APD) treatment improves the clinical skeletal manifestations of Gaucher's disease

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12 December 2020

Is retransplantation cost effective?

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12 December 2020

Orthotopic liver transplantation in the treatment of complications of type 1 Gaucher disease

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12 December 2020

The Norrbothnian type of Gaucher's disease. Mutation diagnosis as a simple technique for risk determination

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12 December 2020

Successful treatment of bone marrow failure in Gaucher's disease with low-dose modified glucocerebrosidase

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12 December 2020

Phenotypic manifestations of Gaucher disease: clinical features in 48 biochemically verified type 1 patients and comment on type 2 patients

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12 December 2020

Gaucher disease: molecular heterogeneity and phenotype-genotype correlations

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12 December 2020

Deficient activity of glucocerebrosidase in urine from patients with type 1 Gaucher disease

1 reference

12 December 2020

Alglucerase for Gaucher's disease: dose, costs and benefits

1 reference

12 December 2020

Orthotopic liver transplantation in two adults with Niemann-Pick and Gaucher's diseases: implications for the treatment of inherited metabolic disease

1 reference

12 December 2020

Comparative study on glucocerebrosidase in spleens from patients with Gaucher disease

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12 December 2020

Correction of neutrophil chemotaxis defect in patients with Gaucher disease by low-dose enzyme replacement therapy

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12 December 2020

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12 December 2020

RecTL: a complex allele of the glucocerebrosidase gene associated with a mild clinical course of Gaucher disease

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12 December 2020

Pathologic fractures may develop in Gaucher patients receiving enzyme replacement therapy

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12 December 2020

Frequency of carriers of chronic (type I) Gaucher disease in Ashkenazi Jews

1 reference

12 December 2020

How attractive does a new technology have to be to warrant adoption and utilization? Tentative guidelines for using clinical and economic evaluations

1 reference

12 December 2020

South African variants of Gaucher disease

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12 December 2020

LIver abnormalities in patients with Gaucher's disease

1 reference

12 December 2020

Home treatment with intravenous enzyme replacement therapy for Gaucher disease: an international collaborative study of 33 patients

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12 December 2020

Intrafamilial clinical variability of type 1 Gaucher disease in a French-Canadian family

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12 December 2020

Allogenic bone marrow transplantation in severe Gaucher disease

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12 December 2020

Consumer costs for genetic services

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12 December 2020

Enzyme replacement therapy of infantile Gaucher disease

1 reference

12 December 2020

Clinical decision making: from theory to practice. Principles for making difficult decisions in difficult times

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12 December 2020

Prediction of severity of Gaucher's disease by identification of mutations at DNA level

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12 December 2020

Enzyme Augmentation in Moderate to Life-Threatening Gaucher Disease

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12 December 2020

Comparative cost of allogeneic or autologous bone marrow transplantation and chemotherapy in patients with acute myeloid leukaemia in first remission

1 reference

12 December 2020

Low-dose enzyme replacement therapy for Gaucher's disease: effects of age, sex, genotype, and clinical features on response to treatment

1 reference

12 December 2020

Treatment of Gaucher's disease

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12 December 2020

Enzyme replacement therapy for Gaucher disease

1 reference

12 December 2020

Treatment of type 1 Gaucher's disease affecting bone with aminohydroxypropylidene bisphosphonate (pamidronate)

1 reference

12 December 2020

Resting energy expenditure in Gaucher's disease type 1: effect of Gaucher's cell burden on energy requirements

1 reference

12 December 2020

Gaucher disease: fate of the splenic remnant after partial splenectomy--a case of rapid enlargement

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12 December 2020

Enzyme therapy in Gaucher disease type 1: dosage efficacy and adverse effects in 33 patients treated for 6 to 24 months

1 reference

12 December 2020

Aminohydroxypropylidene-biphosphonate in the treatment of bone lesions in a case of Gaucher's disease type 3

1 reference

12 December 2020

Molecular screening of Japanese patients with Gaucher disease: phenotypic variability in the same genotypes.

1 reference

12 December 2020

Gaucher disease (Norrbottnian type III): probable founders identified by genealogical and molecular studies

1 reference

12 December 2020

Alglucerase. A review of its therapeutic use in Gaucher's disease

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12 December 2020

Beneficial effect of pre-transplant splenectomy on displacement bone marrow transplantation for Gaucher's syndrome

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12 December 2020

Immunologic and plasma protein studies in a splenic homograft recipient

1 reference

12 December 2020

10.2165/00019053-199507010-00007

Identifiers

DOI

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Dimensions Publication ID

28 July 2017

1011016642

0 references

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