(Q33634963)
Statements
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Home treatment with intravenous enzyme replacement therapy with idursulfase for mucopolysaccharidosis type II - data from the Hunter Outcome Survey (English)
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Barbara K Burton
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Nathalie Guffon
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Jane Roberts
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Ans T van der Ploeg
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Simon A Jones
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HOS investigators
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23 June 2010
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101
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2-3
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123-129
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Identifiers
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