(Q33730464)

29 July 2017

Persistent expression of FLAG-tagged micro dystrophin in nonhuman primates following intramuscular and vascular delivery (English)

1 reference

29 July 2017

Louise R Rodino-Klapac

1

1 reference

29 July 2017

Chrystal L Montgomery

2

1 reference

29 July 2017

William G Bremer

3

1 reference

29 July 2017

Kimberly M Shontz

4

1 reference

29 July 2017

Vinod Malik

5

1 reference

29 July 2017

Nancy Davis

6

1 reference

29 July 2017

Spencer Sprinkle

7

1 reference

29 July 2017

Katherine J Campbell

8

1 reference

29 July 2017

Zarife Sahenk

9

1 reference

29 July 2017

K Reed Clark

10

1 reference

29 July 2017

Christopher M Walker

11

1 reference

29 July 2017

Jerry R Mendell

12

1 reference

29 July 2017

Louis G Chicoine

13

1 reference

29 July 2017

10 November 2009

1 reference

29 July 2017

1 reference

29 July 2017

18

1 reference

29 July 2017

1

1 reference

29 July 2017

109-117

1 reference

describes a project that uses

29 July 2017

ImageQuant

1 reference

11 June 2022

https://www.ebi.ac.uk/europepmc/webservices/rest/PMC2839222/fullTextXML

inferred from PubMed Central ID database lookup

cites work

A preclinical animal model to assess the effect of pre-existing immunity on AAV-mediated gene transfer

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839222

Gene therapy in large animal models of muscular dystrophy

14 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839222

Cardiac expression of a mini-dystrophin that normalizes skeletal muscle force only partially restores heart function in aged Mdx mice.

14 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839222

A single intravenous injection of adeno-associated virus serotype-9 leads to whole body skeletal muscle transduction in dogs.

14 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839222

Adeno-associated virus serotype-9 microdystrophin gene therapy ameliorates electrocardiographic abnormalities in mdx mice.

14 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839222

A translational approach for limb vascular delivery of the micro-dystrophin gene without high volume or high pressure for treatment of Duchenne muscular dystrophy

14 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839222

Gene therapy for duchenne muscular dystrophy: expectations and challenges

14 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839222

Pre-existing AAV capsid-specific CD8+ T cells are unable to eliminate AAV-transduced hepatocytes

14 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839222

rAAV6-microdystrophin preserves muscle function and extends lifespan in severely dystrophic mice.

14 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839222

Adeno-associated virus-mediated microdystrophin expression protects young mdx muscle from contraction-induced injury.

14 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839222

Antigen-independent memory CD8 T cells do not develop during chronic viral infection

14 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839222

Overview of tag protein fusions: from molecular and biochemical fundamentals to commercial systems

14 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839222

Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy

14 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839222

Cross-packaging of a single adeno-associated virus (AAV) type 2 vector genome into multiple AAV serotypes enables transduction with broad specificity

14 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839222

Gene delivery to skeletal muscle results in sustained expression and systemic delivery of a therapeutic protein

14 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839222

Transgenic mdx mice expressing dystrophin with a deletion in the actin-binding domain display a "mild Becker" phenotype

14 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839222

Limb-girdle muscular dystrophy type 2D gene therapy restores alpha-sarcoglycan and associated proteins

14 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839222

Strategies for CNS-directed gene delivery: in vivo gene transfer to the brain using SV40-derived vectors

30 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839222

Efficient transduction of skeletal muscle using vectors based on adeno-associated virus serotype 6.

30 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839222

A new method for recombinant adeno-associated virus vector delivery to murine diaphragm

30 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839222

Modular flexibility of dystrophin: implications for gene therapy of Duchenne muscular dystrophy

30 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839222

Highly purified recombinant adeno-associated virus vectors are biologically active and free of detectable helper and wild-type viruses

30 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839222

Recombinant adeno-associated virus for muscle directed gene therapy

30 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2839222

Mdx respiratory impairment following fibrosis of the diaphragm

30 October 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/19904237

12 December 2020

inferred from PubMed ID database lookup

The mdx mouse diaphragm reproduces the degenerative changes of Duchenne muscular dystrophy

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/19904237

12 December 2020

inferred from PubMed ID database lookup

Systemic administration of micro-dystrophin restores cardiac geometry and prevents dobutamine-induced cardiac pump failure

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/19904237

12 December 2020

inferred from PubMed ID database lookup

A Short Polypeptide Marker Sequence Useful for Recombinant Protein Identification and Purification

1 reference

Crossref

https://api.crossref.org/works/10.1038%2FMT.2009.254

7 January 2021

inferred from DOI database lookup

Identifiers

DOI

10.1038/MT.2009.254

1 reference

29 July 2017

1 reference

29 July 2017

1 reference