(Q33928360)
Statements
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Evaluation of miglustat treatment in patients with type III mucopolysaccharidosis: a randomized, double-blind, placebo-controlled study (English)
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Nathalie Guffon
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Sylvie Bin-Dorel
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Evelyne Decullier
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Carole Paillet
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Jérôme Guitton
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Alain Fouilhoux
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Identifiers
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