(Q33975113)

30 July 2017

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title

Current status of gene therapy for cystic fibrosis pulmonary disease (English)

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30 July 2017

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Mary Jayne Kennedy

1

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30 July 2017

1 January 2002

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Treatments in Respiratory Medicine

30 July 2017

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30 July 2017

1

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30 July 2017

349-360

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30 July 2017

5

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https://scigraph.springernature.com/pub.10.1007/bf03256628

30 July 2017

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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A clinical inflammatory syndrome attributable to aerosolized lipid-DNA administration in cystic fibrosis

21 January 2018

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21 January 2018

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Inhibition of recombinant adeno-associated virus (rAAV) transduction by bronchial secretions from cystic fibrosis patients

21 January 2018

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Enhanced in vivo airway gene transfer via transient modification of host barrier properties with a surface-active agent

21 January 2018

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https://api.crossref.org/works/10.1007%2FBF03256628

Recombinant IL-12 prevents formation of blocking IgA antibodies to recombinant adenovirus and allows repeated gene therapy to mouse lung.

21 January 2018

1 reference

https://api.crossref.org/works/10.1007%2FBF03256628

"Stealth" adenoviruses blunt cell-mediated and humoral immune responses against the virus and allow for significant gene expression upon readministration in the lung

21 January 2018

1 reference

https://api.crossref.org/works/10.1007%2FBF03256628

Strategies to adapt adenoviral vectors for targeted delivery

21 January 2018

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https://api.crossref.org/works/10.1007%2FBF03256628

A novel peptide, THALWHT, for the targeting of human airway epithelia

21 January 2018

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https://api.crossref.org/works/10.1007%2FBF03256628

Engineering novel cell surface receptors for virus-mediated gene transfer

21 January 2018

1 reference

https://api.crossref.org/works/10.1007%2FBF03256628

Prospects for in utero human gene therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1007%2FBF03256628

In utero gene therapy: the case for.

21 January 2018

1 reference

https://api.crossref.org/works/10.1007%2FBF03256628

In utero gene transfer into the pulmonary epithelium

21 January 2018

1 reference

https://api.crossref.org/works/10.1007%2FBF03256628

Foetal gene delivery in mice by intra-amniotic administration of retroviral producer cells and adenovirus

21 January 2018

1 reference

https://api.crossref.org/works/10.1007%2FBF03256628

Reversal of cystic fibrosis phenotype in mice by gene therapy in utero

21 January 2018

1 reference

https://api.crossref.org/works/10.1007%2FBF03256628

Cystic fibrosis: molecular biology and therapeutic implications

21 January 2018

1 reference

https://api.crossref.org/works/10.1007%2FBF03256628

Liposome-mediated CFTR gene transfer to the nasal epithelium of patients with cystic fibrosis

21 January 2018

1 reference

https://api.crossref.org/works/10.1007%2FBF03256628

21 January 2018

Identifiers

DOI

10.1007/BF03256628

1 reference

30 July 2017

1 reference

PubMed ID

14720037