(Q34126901)

31 July 2017

title

Improvement of the mdx mouse dystrophic phenotype by systemic in utero AAV8 delivery of a minidystrophin gene (English)

1 reference

31 July 2017

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1 reference

B M Koppanati

1

1 reference

31 July 2017

J Li

2

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31 July 2017

D P Reay

3

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31 July 2017

B Wang

4

1 reference

31 July 2017

M Daood

5

1 reference

31 July 2017

H Zheng

6

1 reference

31 July 2017

X Xiao

7

1 reference

31 July 2017

J F Watchko

8

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31 July 2017

P R Clemens

9

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31 July 2017

publication date

10 June 2010

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31 July 2017

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31 July 2017

volume

17

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31 July 2017

issue

11

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31 July 2017

page(s)

1355-1362

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Systemic delivery of AAV8 in utero results in gene expression in diaphragm and limb muscle: treatment implications for muscle disorders

31 July 2017

cites work

1 reference

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Analysis of AAV serotypes 1-9 mediated gene expression and tropism in mice after systemic injection

5 July 2018

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A translational approach for limb vascular delivery of the micro-dystrophin gene without high volume or high pressure for treatment of Duchenne muscular dystrophy

5 July 2018

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Cellular heterogeneity during vertebrate skeletal muscle development

5 July 2018

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Fetal gene therapy of alpha-thalassemia in a mouse model

5 July 2018

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rAAV6-microdystrophin preserves muscle function and extends lifespan in severely dystrophic mice.

5 July 2018

1 reference

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Robust systemic transduction with AAV9 vectors in mice: efficient global cardiac gene transfer superior to that of AAV8.

5 July 2018

1 reference

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Adeno-associated virus-mediated microdystrophin expression protects young mdx muscle from contraction-induced injury.

5 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2939256

Efficacy of an adeno-associated virus 8-pseudotyped vector in glycogen storage disease type II.

5 July 2018

1 reference

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Systemic delivery of genes to striated muscles using adeno-associated viral vectors.

5 July 2018

1 reference

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Rescue of enzyme deficiency in embryonic diaphragm in a mouse model of metabolic myopathy: Pompe disease

5 July 2018

1 reference

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The formation of skeletal muscle: from somite to limb

5 July 2018

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Functional characteristics of dystrophic skeletal muscle: insights from animal models

5 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2939256

Function and genetics of dystrophin and dystrophin-related proteins in muscle

5 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2939256

The dystrophin-glycoprotein complex, cellular signaling, and the regulation of cell survival in the muscular dystrophies

5 July 2018

1 reference

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A new blocking method for application of murine monoclonal antibody to mouse tissue sections

5 July 2018

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Production of high-titer recombinant adeno-associated virus vectors in the absence of helper adenovirus

5 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2939256

Role for highly regulated rep gene expression in adeno-associated virus vector production

5 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2939256

The basal lamina is a physical barrier to herpes simplex virus-mediated gene delivery to mature muscle fibers.

5 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2939256

Organogenesis of the mouse extensor digitorum logus muscle: a quantitative study

5 July 2018

1 reference

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The organogenesis of murine striated muscle: a cytoarchitectural study

5 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2939256

Cytoarchitecture of the fetal murine soleus muscle

5 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2939256

Cellular insertion of primary and secondary myotubes in embryonic rat muscles.

5 July 2018

1 reference

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Population frequencies of inherited neuromuscular diseases—A world survey

5 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2939256

AAV vector-mediated microdystrophin expression in a relatively small percentage of mdx myofibers improved the mdx phenotype

5 July 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.84

Antisense oligonucleotide-induced exon skipping restores dystrophin expression in vitro in a canine model of DMD.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.84

Dystrophic phenotype of canine X-linked muscular dystrophy is mitigated by adenovirus-mediated utrophin gene transfer.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.84

Adeno-associated virus serotype 8 efficiently delivers genes to muscle and heart

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.84

Permanent phenotypic correction of hemophilia B in immunocompetent mice by prenatal gene therapy.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.84

In utero gene transfer of human factor IX to fetal mice can induce postnatal tolerance of the exogenous clotting factor

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.84

Persistent expression of hF.IX After tolerance induction by in utero or neonatal administration of AAV-1-F.IX in hemophilia B mice

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.84

Full-length dystrophin gene transfer to the mdx mouse in utero

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.84

Genetic correction of the fetal brain increases the lifespan of mice with the severe multisystemic disease mucopolysaccharidosis type VII.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.84

Widespread gene transduction to the central nervous system by adenovirus in utero: implication for prenatal gene therapy to brain involvement of lysosomal storage disease

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.84

Long-term correction of bilirubin UDPglucuronyltransferase deficiency in rats by in utero lentiviral gene transfer

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.84

Reversal of cystic fibrosis phenotype in mice by gene therapy in utero

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.84

Ability of adeno-associated virus serotype 8-mediated hepatic expression of acid alpha-glucosidase to correct the biochemical and motor function deficits of presymptomatic and symptomatic Pompe mice

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.84

Myostatin propeptide gene delivery by adeno-associated virus serotype 8 vectors enhances muscle growth and ameliorates dystrophic phenotypes in mdx mice

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.84

A canine minidystrophin is functional and therapeutic in mdx mice

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.84

Comparison of high-capacity and first-generation adenoviral vector gene delivery to murine muscle in utero

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FGT.2010.84

The mutant mdx: inherited myopathy in the mouse. Morphological studies of nerves, muscles and end-plates

21 January 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/20535217

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/20535217

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Aging normal and dystrophic mouse muscle: analysis of myogenicity in cultures of living single fibers

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/20535217

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Identifiers

DOI

10.1038/GT.2010.84

1 reference

31 July 2017

1 reference

31 July 2017

1 reference