(Q34433586)

2 August 2017

title

Prevention of muscular dystrophy in mice by CRISPR/Cas9-mediated editing of germline DNA (English)

1 reference

2 August 2017

0 references

1 reference

1 reference

Chengzu Long

1

1 reference

2 August 2017

John R McAnally

2

1 reference

2 August 2017

John M Shelton

3

1 reference

2 August 2017

Alex A Mireault

4

1 reference

2 August 2017

Rhonda Bassel-Duby

5

1 reference

2 August 2017

Eric N Olson

6

1 reference

2 August 2017

language of work or name

English

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publication date

14 August 2014

1 reference

2 August 2017

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2 August 2017

volume

345

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2 August 2017

issue

6201

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2 August 2017

page(s)

1184-1188

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Somatic mosaicism and allele complexity induced by CRISPR/Cas9 RNA injections in mouse zygotes

2 August 2017

cites work

1 reference

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Genome-wide identification of CRISPR/Cas9 off-targets in human genome

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4398027

Development and applications of CRISPR-Cas9 for genome engineering

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4398027

Engineering adeno-associated viruses for clinical gene therapy

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4398027

Genome-wide analysis reveals characteristics of off-target sites bound by the Cas9 endonuclease.

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4398027

Genome-wide binding of the CRISPR endonuclease Cas9 in mammalian cells

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4398027

Genome editing with Cas9 in adult mice corrects a disease mutation and phenotype.

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4398027

Correction of a genetic disease in mouse via use of CRISPR-Cas9.

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4398027

Functional repair of CFTR by CRISPR/Cas9 in intestinal stem cell organoids of cystic fibrosis patients

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4398027

Cas9 as a versatile tool for engineering biology

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4398027

Revertant fibers in the mdx murine model of Duchenne muscular dystrophy: an age- and muscle-related reappraisal

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4398027

Modified mRNA directs the fate of heart progenitor cells and induces vascular regeneration after myocardial infarction

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4398027

One-step generation of mice carrying reporter and conditional alleles by CRISPR/Cas-mediated genome engineering

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4398027

High-throughput profiling of off-target DNA cleavage reveals RNA-programmed Cas9 nuclease specificity

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4398027

High-frequency off-target mutagenesis induced by CRISPR-Cas nucleases in human cells

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4398027

Reading frame correction by targeted genome editing restores dystrophin expression in cells from Duchenne muscular dystrophy patients.

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4398027

One-step generation of mice carrying mutations in multiple genes by CRISPR/Cas-mediated genome engineering

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4398027

TALEN-based gene correction for epidermolysis bullosa.

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4398027

Satellite cells and the muscle stem cell niche

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4398027

RNA-guided human genome engineering via Cas9

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4398027

Multiplex genome engineering using CRISPR/Cas systems

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4398027

A Programmable Dual-RNA-Guided DNA Endonuclease in Adaptive Bacterial Immunity

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4398027

Long-term safety and efficacy following systemic administration of a self-complementary AAV vector encoding human FIX pseudotyped with serotype 5 and 8 capsid proteins.

6 July 2018

1 reference

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Tissue-specific gene delivery via nanoparticle coating

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4398027

Highly efficient endogenous human gene correction using designed zinc-finger nucleases

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4398027

Advances in Duchenne muscular dystrophy gene therapy

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4398027

X chromosome-linked muscular dystrophy (mdx) in the mouse

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4398027

Genetics of Duchenne muscular dystrophy

6 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4398027

Therapy for Duchenne muscular dystrophy: renewed optimism from genetic approaches

6 July 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCIENCE.1254445

Direct isolation of satellite cells for skeletal muscle regeneration.

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCIENCE.1254445

Expression of therapeutic proteins after delivery of chemically modified mRNA in mice

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCIENCE.1254445

Characterization of 65 epitope-specific dystrophin monoclonal antibodies in canine and murine models of duchenne muscular dystrophy by immunostaining and western blot

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCIENCE.1254445

Satellite cells, connective tissue fibroblasts and their interactions are crucial for muscle regeneration.

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCIENCE.1254445

Laser-assisted microdissection of membrane-mounted paraffin sections for polymerase chain reaction analysis: identification of cell populations using immunohistochemistry and in situ hybridization.

21 January 2018

1 reference

https://api.crossref.org/works/10.1126%2FSCIENCE.1254445

The molecular basis of muscular dystrophy in the mdx mouse: a point mutation

21 January 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/25123483

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

In vivo plasmid DNA electroporation resulted in transfection of satellite cells and lasting transgene expression in regenerated muscle fibers

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/25123483

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Identifiers

DOI

10.1126/SCIENCE.1254445

1 reference

2 August 2017

1 reference

2 August 2017

1 reference