(Q34979802)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25363772%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

title

Promoterless gene targeting without nucleases ameliorates haemophilia B in mice (English)

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25363772%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

0 references

0 references

1 reference

2

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25363772%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

Paul N. Valdmanis

7

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25363772%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

author name string

A Barzel

1

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25363772%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

Y Shi

3

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25363772%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

Y Huang

4

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25363772%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

K Chu

5

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25363772%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

F Zhang

6

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25363772%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

L P Spector

8

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25363772%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

M H Porteus

9

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25363772%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

K M Gaensler

10

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25363772%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

M A Kay

11

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25363772%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

language of work or name

English

0 references

publication date

29 October 2014

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25363772%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25363772%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

volume

517

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25363772%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

issue

7534

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25363772%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

page(s)

360-364

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25363772%20AND%20SRC:MED&resulttype=core&format=json

https://scigraph.springernature.com/pub.10.1038/nature13864

22 February 2020

exact match

0 references

cites work

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8 July 2018

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Selection and evaluation of clinically relevant AAV variants in a xenograft liver model

8 July 2018

1 reference

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Analysis of off-target effects of CRISPR/Cas-derived RNA-guided endonucleases and nickases.

8 July 2018

1 reference

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8 July 2018

1 reference

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Lentiviral hematopoietic stem cell gene therapy in patients with Wiskott-Aldrich syndrome.

8 July 2018

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High-frequency off-target mutagenesis induced by CRISPR-Cas nucleases in human cells

8 July 2018

1 reference

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Role of antigen-specific regulatory CD4+CD25+ T cells in tolerance induction after neonatal IP administration of AAV-hF.IX.

8 July 2018

1 reference

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ZFN, TALEN, and CRISPR/Cas-based methods for genome engineering

8 July 2018

1 reference

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A mini-intronic plasmid (MIP): a novel robust transgene expression vector in vivo and in vitro

8 July 2018

1 reference

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Albumin: pathophysiologic basis of its role in the treatment of cirrhosis and its complications

8 July 2018

1 reference

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Mechanisms of retroviral integration and mutagenesis

8 July 2018

1 reference

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Ribosomal DNA integrating rAAV-rDNA vectors allow for stable transgene expression.

8 July 2018

1 reference

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Single amino acid modification of adeno-associated virus capsid changes transduction and humoral immune profiles

8 July 2018

1 reference

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AAV-mediated gene targeting is significantly enhanced by transient inhibition of nonhomologous end joining or the proteasome in vivo

8 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4297598

Adenovirus-associated virus vector-mediated gene transfer in hemophilia B

8 July 2018

1 reference

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Antibody-based protection against HIV infection by vectored immunoprophylaxis

8 July 2018

1 reference

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In vivo genome editing restores haemostasis in a mouse model of haemophilia

8 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4297598

High cleavage efficiency of a 2A peptide derived from porcine teschovirus-1 in human cell lines, zebrafish and mice

8 July 2018

1 reference

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Adeno-associated virus gene repair corrects a mouse model of hereditary tyrosinemia in vivo.

8 July 2018

1 reference

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Organogenesis and development of the liver

8 July 2018

1 reference

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Gene therapy with human and mouse T-cell receptors mediates cancer regression and targets normal tissues expressing cognate antigen

8 July 2018

1 reference

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Insertional oncogenesis in 4 patients after retrovirus-mediated gene therapy of SCID-X1

8 July 2018

1 reference

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In vitro and in vivo gene therapy vector evolution via multispecies interbreeding and retargeting of adeno-associated viruses

8 July 2018

1 reference

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Fatality in mice due to oversaturation of cellular microRNA/short hairpin RNA pathways

8 July 2018

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Liver transduction with recombinant adeno-associated virus is primarily restricted by capsid serotype not vector genotype

8 July 2018

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Unrestricted hepatocyte transduction with adeno-associated virus serotype 8 vectors in mice

8 July 2018

1 reference

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Extrachromosomal recombinant adeno-associated virus vector genomes are primarily responsible for stable liver transduction in vivo

8 July 2018

1 reference

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AAV vector integration sites in mouse hepatocellular carcinoma.

8 July 2018

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Gene targeting in vivo by adeno-associated virus vectors.

21 January 2018

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In vivo-directed evolution of a new adeno-associated virus for therapeutic outer retinal gene delivery from the vitreous

21 January 2018

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Robust ZFN-mediated genome editing in adult hemophilic mice.

21 January 2018

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A reproducible and well-tolerated method for 2/3 partial hepatectomy in mice

21 January 2018

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Optimal Immunofluorescent Staining for Human Factor IX and Infiltrating T Cells following Gene Therapy for Hemophilia B.

21 January 2018

1 reference

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Gene therapy for lysosomal storage disorders

26 October 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/25363772

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Identifiers

DOI

10.1038/NATURE13864

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25363772%20AND%20SRC:MED&resulttype=core&format=json

Dimensions Publication ID

22 February 2020

0 references

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25363772%20AND%20SRC:MED&resulttype=core&format=json

22 February 2020

PubMed publication ID

25363772

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:25363772%20AND%20SRC:MED&resulttype=core&format=json