(Q35566831)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:14575721%20AND%20SRC:MED&resulttype=core&format=json

20 December 2019

review article

1 reference

title

Adeno-associated viral vectors for retinal gene transfer (English)

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:14575721%20AND%20SRC:MED&resulttype=core&format=json

20 December 2019

1

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:14575721%20AND%20SRC:MED&resulttype=core&format=json

20 December 2019

Alberto Auricchio

series ordinal

2

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:14575721%20AND%20SRC:MED&resulttype=core&format=json

20 December 2019

author name string

Enrico M Surace

series ordinal

1

1 reference

8 August 2017

Alberto Auricchio

series ordinal

2

1 reference

8 August 2017

1 November 2003

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:14575721%20AND%20SRC:MED&resulttype=core&format=json

Progress in Retinal and Eye Research

20 December 2019

published in

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:14575721%20AND%20SRC:MED&resulttype=core&format=json

20 December 2019

volume

22

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:14575721%20AND%20SRC:MED&resulttype=core&format=json

20 December 2019

issue

6

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:14575721%20AND%20SRC:MED&resulttype=core&format=json

20 December 2019

page(s)

705-719

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:14575721%20AND%20SRC:MED&resulttype=core&format=json

Gene transfer into the mouse retina mediated by an adeno-associated viral vector

20 December 2019

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Adeno-associated virus gene transfer to mouse retina

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7 January 2021

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7 January 2021

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7 January 2021

A deviant immune response to viral proteins and transgene product is generated on subretinal administration of adenovirus and adeno-associated virus

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7 January 2021

Exchange of surface proteins impacts on viral vector cellular specificity and transduction characteristics: the retina as a model

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7 January 2021

Inhibition of retinal neovascularization by intraocular viral-mediated delivery of anti-angiogenic agents

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7 January 2021

Noninvasive gene transfer to the lung for systemic delivery of therapeutic proteins.

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7 January 2021

Pharmacological regulation of protein expression from adeno-associated viral vectors in the eye.

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7 January 2021

Inhibition of retinal neovascularisation by gene transfer of soluble VEGF receptor sFlt-1.

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7 January 2021

Retinal rod photoreceptor-specific gene mutation perturbs cone pathway development.

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7 January 2021

Characterization of the DNA of a defective human parvovirus isolated from a genital site

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7 January 2021

Targeted adeno-associated virus vector transduction of nonpermissive cells mediated by a bispecific F(ab'gamma)2 antibody

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7 January 2021

Gene therapy for ocular disease

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7 January 2021

Humoral response after administration of E1-deleted adenoviruses: immune privilege of the subretinal space

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7 January 2021

Adenovirus-mediated delivery of rhodopsin-promoted bcl-2 results in a delay in photoreceptor cell death in the rd/rd mouse

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7 January 2021

Stable transgene expression in rod photoreceptors after recombinant adeno-associated virus-mediated gene transfer to monkey retina

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7 January 2021

Effects of adeno-associated virus-vectored ciliary neurotrophic factor on retinal structure and function in mice with a P216L rds/peripherin mutation

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7 January 2021

Retinal and choroidal neovascularization

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7 January 2021

Angiogenesis in cancer and other diseases

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7 January 2021

Intraocular gene transfer of ciliary neurotrophic factor prevents death and increases responsiveness of rod photoreceptors in the retinal degeneration slow mouse

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7 January 2021

Retinal degeneration mutants in the mouse

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7 January 2021

Apoptosis: final common pathway of photoreceptor death in rd, rds, and rhodopsin mutant mice

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7 January 2021

Persistent expression of canine factor IX in hemophilia B canines

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7 January 2021

Several log increase in therapeutic transgene delivery by distinct adeno-associated viral serotype vectors

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7 January 2021

bcl-2 overexpression reduces apoptotic photoreceptor cell death in three different retinal degenerations

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7 January 2021

Molecular genetics of Leber congenital amaurosis

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7 January 2021

Neonatal gene transfer leads to widespread correction of pathology in a murine model of lysosomal storage disease.

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7 January 2021

Recombinant adeno-associated virus type 2, 4, and 5 vectors: transduction of variant cell types and regions in the mammalian central nervous system.

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7 January 2021

Gene therapy and retinitis pigmentosa: advances and future challenges

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7 January 2021

Pharmacologically regulated gene expression in the retina following transduction with viral vectors

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7 January 2021

The chemical repertoire of natural ribozymes

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7 January 2021

Structural and functional heterogeneity of integrated recombinant AAV genomes

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7 January 2021

Enhancement of muscle gene delivery with pseudotyped adeno-associated virus type 5 correlates with myoblast differentiation.

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https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Expanding AAV packaging capacity with trans-splicing or overlapping vectors: a quantitative comparison

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7 January 2021

Persistent transgene product in retina, optic nerve and brain after intraocular injection of rAAV.

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7 January 2021

Peroral gene therapy of lactose intolerance using an adeno-associated virus vector

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7 January 2021

An oral vaccine against NMDAR1 with efficacy in experimental stroke and epilepsy

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7 January 2021

On the genetics of retinitis pigmentosa and on mutation-independent approaches to therapeutic intervention

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7 January 2021

Efficient photoreceptor-targeted gene expression in vivo by recombinant adeno-associated virus

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7 January 2021

Correction of the enzymatic and functional deficits in a model of Pompe disease using adeno-associated virus vectors

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7 January 2021

Neurological correction of lysosomal storage in a mucopolysaccharidosis IIIB mouse model by adeno-associated virus-mediated gene delivery

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7 January 2021

Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy

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7 January 2021

Genetic capsid modifications allow efficient re-targeting of adeno-associated virus type 2.

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7 January 2021

Defective subunit assembly underlies a digenic form of retinitis pigmentosa linked to mutations in peripherin/rds and rom-1.

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7 January 2021

Subunit composition of the peripherin/rds-rom-1 disk rim complex from rod photoreceptors: hydrodynamic evidence for a tetrameric quaternary structure

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7 January 2021

Two animal models of retinal degeneration are rescued by recombinant adeno-associated virus-mediated production of FGF-5 and FGF-18.

1 reference

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7 January 2021

Adeno-associated viral-mediated catalase expression suppresses optic neuritis in experimental allergic encephalomyelitis

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7 January 2021

Reporter expression persists 1 year after adeno-associated virus-mediated gene transfer to the optic nerve

1 reference

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7 January 2021

Rescue of a mitochondrial deficiency causing Leber Hereditary Optic Neuropathy

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7 January 2021

Evidence for two apoptotic pathways in light-induced retinal degeneration

1 reference

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7 January 2021

Modification of glial-neuronal cell interactions prevents photoreceptor apoptosis during light-induced retinal degeneration.

1 reference

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7 January 2021

Intravitreal injection of adeno-associated viral vectors results in the transduction of different types of retinal neurons in neonatal and adult rats: a comparison with lentiviral vectors.

1 reference

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7 January 2021

Ribozyme uses in retinal gene therapy.

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7 January 2021

Development and degeneration of retina in rds mutant mice: photoreceptor abnormalities in the heterozygotes

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7 January 2021

Adeno-associated virus expresses transgenes in hair follicles and epidermis

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7 January 2021

Stable gene transfer and expression of human blood coagulation factor IX after intramuscular injection of recombinant adeno-associated virus

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7 January 2021

Hybrid vectors based on adeno-associated virus serotypes 2 and 5 for muscle-directed gene transfer

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7 January 2021

Phenotypic rescue after adeno-associated virus-mediated delivery of 4-sulfatase to the retinal pigment epithelium of feline mucopolysaccharidosis VI.

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Chronic suppression of heart-failure progression by a pseudophosphorylated mutant of phospholamban via in vivo cardiac rAAV gene delivery

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7 January 2021

BDNF regulates the maturation of inhibition and the critical period of plasticity in mouse visual cortex.

1 reference

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7 January 2021

High-fidelity correction of mutations at multiple chromosomal positions by adeno-associated virus vectors.

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7 January 2021

Introduction of single base substitutions at homologous chromosomal sequences by adeno-associated virus vectors

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7 January 2021

Clinical protocol. Gene therapy of Canavan disease: AAV-2 vector for neurosurgical delivery of aspartoacylase gene (ASPA) to the human brain

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7 January 2021

Cochlear gene delivery through an intact round window membrane in mouse

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7 January 2021

Long-term gene expression and phenotypic correction using adeno-associated virus vectors in the mammalian brain

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7 January 2021

Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector.

1 reference

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7 January 2021

Non-cell-autonomous photoreceptor degeneration in rds mutant mice mosaic for expression of a rescue transgene

1 reference

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7 January 2021

Deficiency of rds/peripherin causes photoreceptor death in mouse models of digenic and dominant retinitis pigmentosa

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Safety of adeno-associated virus as cochlear gene transfer vector: analysis of distant spread beyond injected cochleae

1 reference

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7 January 2021

Filovirus-pseudotyped lentiviral vector can efficiently and stably transduce airway epithelia in vivo

1 reference

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7 January 2021

Persistent expression of human clotting factor IX from mouse liver after intravenous injection of adeno-associated virus vectors

1 reference

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7 January 2021

Encapsidated adenovirus mini-chromosome-mediated delivery of genes to the retina: application to the rescue of photoreceptor degeneration

1 reference

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7 January 2021

Potential long-term inhibition of ocular neovascularisation by recombinant adeno-associated virus-mediated secretion gene therapy

1 reference

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7 January 2021

Green fluorescent protein as a reporter for gene transfer studies in the cochlea

1 reference

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7 January 2021

Long-term in vivo cochlear transgene expression mediated by recombinant adeno-associated virus

1 reference

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7 January 2021

Gene therapy for hemophilia B: AAV-mediated transfer of the gene for coagulation factor IX to human muscle.

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Ribozyme rescue of photoreceptor cells in P23H transgenic rats: long-term survival and late-stage therapy.

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Adeno-associated virus: a vector system for efficient introduction and integration of DNA into a variety of mammalian cell types

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Ribozyme rescue of photoreceptor cells in a transgenic rat model of autosomal dominant retinitis pigmentosa.

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Long-term protection of retinal structure but not function using RAAV.CNTF in animal models of retinitis pigmentosa

1 reference

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7 January 2021

AAV-mediated delivery of ciliary neurotrophic factor prolongs photoreceptor survival in the rhodopsin knockout mouse

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Adenoviral and adeno-associated viral vector mediated gene transfer in the guinea pig cochlea

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Canine inherited retinal degenerations: update on molecular genetic research and its clinical application

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Site-specific integration by adeno-associated virus

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Cochlear function and transgene expression in the guinea pig cochlea, using adenovirus- and adeno-associated virus-directed gene transfer.

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Midbrain injection of recombinant adeno-associated virus encoding rat glial cell line-derived neurotrophic factor protects nigral neurons in a progressive 6-hydroxydopamine-induced degeneration model of Parkinson's disease in rats

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

AAV-mediated factor IX gene transfer to skeletal muscle in patients with severe hemophilia B.

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Gene delivery to the eye using adeno-associated viral vectors

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Glial cell line derived neurotrophic factor delays photoreceptor degeneration in a transgenic rat model of retinitis pigmentosa

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Recombinant AAV-mediated delivery of a tet-inducible reporter gene to the rat retina

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Baculoviral IAP repeat-containing-4 protects optic nerve axons in a rat glaucoma model

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Gene therapy strategy for long-term myocardial protection using adeno-associated virus-mediated delivery of heme oxygenase gene

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Stable and efficient gene transfer into the retina using an HIV-based lentiviral vector

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

An AAV-derived Apaf-1 dominant negative inhibitor prevents MPTP toxicity as antiapoptotic gene therapy for Parkinson's disease

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Normal retina releases a diffusible factor stimulating cone survival in the retinal degeneration mouse

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Direct intramuscular injection with recombinant AAV vectors results in sustained expression in a dog model of hemophilia

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Behavioral recovery in a primate model of Parkinson's disease by triple transduction of striatal cells with adeno-associated viral vectors expressing dopamine-synthesizing enzymes

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Increasing the size of rAAV-mediated expression cassettes in vivo by intermolecular joining of two complementary vectors

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Transgenic mice with a rhodopsin mutation (Pro23His): a mouse model of autosomal dominant retinitis pigmentosa

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Pathways to photoreceptor cell death in inherited retinal degenerations

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Vascular endothelial growth factor/vascular permeability factor expression in a mouse model of retinal neovascularization

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Lack of site-specific integration of the recombinant adeno-associated virus 2 genomes in human cells

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Adeno-associated virus expression systems for gene transfer

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

The adeno-associated virus crystal: impact inversely proportional to size

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Cross-packaging of a single adeno-associated virus (AAV) type 2 vector genome into multiple AAV serotypes enables transduction with broad specificity

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Adeno-associated virus type-2 expression of pigmented epithelium-derived factor or Kringles 1-3 of angiostatin reduce retinal neovascularization

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Site-specific integration mediated by a hybrid adenovirus/adeno-associated virus vector.

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Efficient trans-splicing in the retina expands the utility of adeno-associated virus as a vector for gene therapy.

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Retinitis pigmentosa and allied diseases: numerous diseases, genes, and inheritance patterns.

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Evaluation of adeno-associated virus-mediated gene transfer into the rat retina by clinical fluorescence photography

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Long-term real-time monitoring of adeno-associated virus-mediated gene expression in the rat retina

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Human gene targeting by viral vectors

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Validation of AAV-mediated gene targeting

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Functional effect of adeno-associated virus mediated gene transfer of aromatic L-amino acid decarboxylase into the striatum of 6-OHDA-lesioned rats.

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Gene replacement therapy in the retinal degeneration slow (rds) mouse: the effect on retinal degeneration following partial transduction of the retina

1 reference

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7 January 2021

Kinetics of transgene expression in mouse retina following sub-retinal injection of recombinant adeno-associated virus

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Triple transduction with adeno-associated virus vectors expressing tyrosine hydroxylase, aromatic-L-amino-acid decarboxylase, and GTP cyclohydrolase I for gene therapy of Parkinson's disease

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Sustained production of beta-glucuronidase from localized sites after AAV vector gene transfer results in widespread distribution of enzyme and reversal of lysosomal storage lesions in a large volume of brain in mucopolysaccharidosis VII mice.

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Persistent and therapeutic concentrations of human factor IX in mice after hepatic gene transfer of recombinant AAV vectors

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

ERG and EOG abnormalities in carriers of X-linked retinitis pigmentosa

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Membrane-associated heparan sulfate proteoglycan is a receptor for adeno-associated virus type 2 virions

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

AlphaVbeta5 integrin: a co-receptor for adeno-associated virus type 2 infection

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Long-term systemic therapy of Fabry disease in a knockout mouse by adeno-associated virus-mediated muscle-directed gene transfer

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Site-specific integration of a transgene mediated by a hybrid adenovirus/adeno-associated virus vector using the Cre/loxP-expression-switching system

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Sustained correction of bleeding disorder in hemophilia B mice by gene therapy

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Sustained expression of therapeutic level of factor IX in hemophilia B dogs by AAV-mediated gene therapy in liver

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Mutational analysis of the adeno-associated virus type 2 (AAV2) capsid gene and construction of AAV2 vectors with altered tropism

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

The atomic structure of adeno-associated virus (AAV-2), a vector for human gene therapy.

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Trans-splicing vectors expand the utility of adeno-associated virus for gene therapy

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Virus-mediated transduction of murine retina with adeno-associated virus: effects of viral capsid and genome size.

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Adeno-associated virus type 5 (AAV5) but not AAV2 binds to the apical surfaces of airway epithelia and facilitates gene transfer

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

Birth and death in the retina: more related than we thought?

1 reference

https://api.crossref.org/works/10.1016%2FS1350-9462%2803%2900052-1

7 January 2021

10.1016/S1350-9462(03)00052-1

Identifiers

DOI

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:14575721%20AND%20SRC:MED&resulttype=core&format=json

20 December 2019

1 reference