(Q35586463)

English

Systemic correction of the muscle disorder glycogen storage disease type II after hepatic targeting of a modified adenovirus vector encoding human acid-alpha-glucosidase

scientific article published on August 1999

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scholarly article

1 reference

Europe PubMed Central

PubMed publication ID

9 August 2017

Systemic correction of the muscle disorder glycogen storage disease type II after hepatic targeting of a modified adenovirus vector encoding human acid-alpha-glucosidase (English)

1 reference

Europe PubMed Central

PubMed publication ID

9 August 2017

vector-borne disease

0 references

1 reference

based on heuristic

inferred from title

glycogen storage disease

1 reference

based on heuristic

inferred from title

Thomas L. Dawson

4

1 reference

Europe PubMed Central

PubMed publication ID

9 August 2017

author name string

Amalfitano A

1

1 reference

Europe PubMed Central

PubMed publication ID

9 August 2017

McVie-Wylie AJ

2

1 reference

Europe PubMed Central

PubMed publication ID

9 August 2017

Hu H

3

1 reference

Europe PubMed Central

PubMed publication ID

9 August 2017

Raben N

5

1 reference

Europe PubMed Central

PubMed publication ID

9 August 2017

Plotz P

6

1 reference

Europe PubMed Central

PubMed publication ID

9 August 2017

Chen YT

7

1 reference

Europe PubMed Central

PubMed publication ID

9 August 2017

language of work or name

0 references

publication date

1 August 1999

1 reference

Europe PubMed Central

PubMed publication ID

9 August 2017

number of pages

6

1 reference

based on heuristic

inferred from page(s)

Proceedings of the National Academy of Sciences of the United States of America

1 reference

Europe PubMed Central

PubMed publication ID

9 August 2017

96

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Europe PubMed Central

PubMed publication ID

9 August 2017

16

1 reference

Europe PubMed Central

PubMed publication ID

9 August 2017

8861-8866

1 reference

Europe PubMed Central

PubMed publication ID

9 August 2017

Adenovirus-mediated transfer of human acid maltase gene reduces glycogen accumulation in skeletal muscle of Japanese quail with acid maltase deficiency

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=17698

27 July 2018

Targeted disruption of the acid alpha-glucosidase gene in mice causes an illness with critical features of both infantile and adult human glycogen storage disease type II

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=17698

27 July 2018

Similarity of strain- and route-dependent murine responses to an adenovirus vector using the homologous thrombopoietin cDNA as the reporter genes

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=17698

27 July 2018

Clinical and metabolic correction of pompe disease by enzyme therapy in acid maltase-deficient quail

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=17698

27 July 2018

Production and characterization of improved adenovirus vectors with the E1, E2b, and E3 genes deleted

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=17698

27 July 2018

Reactivation of the previously silenced cytomegalovirus major immediate-early promoter in the mouse liver: involvement of NFkappaB.

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=17698

27 July 2018

Generalized glycogen storage and cardiomegaly in a knockout mouse model of Pompe disease

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=17698

27 July 2018

Isolation and characterization of packaging cell lines that coexpress the adenovirus E1, DNA polymerase, and preterminal proteins: implications for gene therapy

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=17698

27 July 2018

Evaluation of promoter strength for hepatic gene expression in vivo following adenovirus-mediated gene transfer

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=17698

27 July 2018

Immune responses to transgene-encoded proteins limit the stability of gene expression after injection of replication-defective adenovirus vectors

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=17698

27 July 2018

High-level production of recombinant human lysosomal acid alpha-glucosidase in Chinese hamster ovary cells which targets to heart muscle and corrects glycogen accumulation in fibroblasts from patients with Pompe disease

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=17698

27 July 2018

Assessment of recombinant adenoviral vectors for hepatic gene therapy

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=17698

27 July 2018

The impact of developmental stage, route of administration and the immune system on adenovirus-mediated gene transfer

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=17698

27 July 2018

Widespread long-term gene transfer to mouse skeletal muscles and heart

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=17698

27 July 2018

Persistence of an [E1-, polymerase-] adenovirus vector despite transduction of a neoantigen into immune-competent mice

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=17698

26 September 2018

Complete correction of acid alpha-glucosidase deficiency in Pompe disease fibroblasts in vitro, and lysosomally targeted expression in neonatal rat cardiac and skeletal muscle

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=17698

26 September 2018

Improved adenovirus packaging cell lines to support the growth of replication-defective gene-delivery vectors

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=17698

26 September 2018

Adenovirus-mediated transfer of the acid alpha-glucosidase gene into fibroblasts, myoblasts and myotubes from patients with glycogen storage disease type II leads to high level expression of enzyme and corrects glycogen accumulation

1 reference

https://pubmed.ncbi.nlm.nih.gov/10430861

12 December 2020

based on heuristic

inferred from PubMed ID database lookup

Recombinant human acid alpha-glucosidase: high level production in mouse milk, biochemical characteristics, correction of enzyme deficiency in GSDII KO mice

1 reference

https://pubmed.ncbi.nlm.nih.gov/10430861

12 December 2020

based on heuristic

inferred from PubMed ID database lookup

A new mutant of Japanese quail (Coturnix coturnix japonica) characterized by generalized glycogenosis

1 reference

https://pubmed.ncbi.nlm.nih.gov/10430861

12 December 2020

based on heuristic

inferred from PubMed ID database lookup

Replacement therapy for inherited enzyme deficiency--macrophage-targeted glucocerebrosidase for Gaucher's disease

1 reference

https://pubmed.ncbi.nlm.nih.gov/10430861

12 December 2020

based on heuristic

inferred from PubMed ID database lookup

A phase 1 study, in cystic fibrosis patients, of the safety, toxicity, and biological efficacy of a single administration of a replication deficient, recombinant adenovirus carrying the cDNA of the normal cystic fibrosis transmembrane conductance reg

1 reference

https://pubmed.ncbi.nlm.nih.gov/10430861

12 December 2020

based on heuristic

inferred from PubMed ID database lookup

Identifiers

10.1073/PNAS.96.16.8861

1 reference

Europe PubMed Central

PubMed publication ID

9 August 2017

1999PNAS...96.8861A

0 references

PMC publication ID

1 reference

Europe PubMed Central

PubMed publication ID

9 August 2017

PubMed publication ID

1 reference

Europe PubMed Central

PubMed publication ID

9 August 2017

ResearchGate publication ID

0 references

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