(Q35659639)

9 August 2017

title

Systemic gene transfer to skeletal muscle using reengineered AAV vectors (English)

1 reference

9 August 2017

Jana L Phillips

1

1 reference

9 August 2017

Julia Hegge

2

1 reference

9 August 2017

Jon A Wolff

3

1 reference

9 August 2017

R Jude Samulski

4

1 reference

9 August 2017

Aravind Asokan

5

1 reference

9 August 2017

language of work or name

English

0 references

publication date

1 January 2011

1 reference

Methods in Molecular Biology

9 August 2017

published in

1 reference

9 August 2017

volume

709

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9 August 2017

page(s)

141-151

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AAV-directed muscular dystrophy gene therapy

9 August 2017

cites work

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3253371

Reengineering a receptor footprint of adeno-associated virus enables selective and systemic gene transfer to muscle

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3253371

Spinal muscular atrophy: molecular mechanisms

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3253371

Musculoskeletal manifestations of lysosomal storage disorders.

12 July 2018

1 reference

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Emerging strategies for cell and gene therapy of the muscular dystrophies

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3253371

Autoimmune myasthenia gravis: emerging clinical and biological heterogeneity

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3253371

Musculoskeletal complications encountered in the lysosomal storage disorders

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3253371

Production of recombinant adeno-associated viral vectors for in vitro and in vivo use.

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3253371

Production and characterization of adeno-associated viral vectors

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3253371

Pathophysiology of duchenne muscular dystrophy: current hypotheses

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3253371

Production and purification of serotype 1, 2, and 5 recombinant adeno-associated viral vectors

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3253371

Cross-packaging of a single adeno-associated virus (AAV) type 2 vector genome into multiple AAV serotypes enables transduction with broad specificity

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3253371

Effect of adeno-associated virus serotype and genomic structure on liver transduction and biodistribution in mice of both genders

12 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3253371

Myodys, a full-length dystrophin plasmid vector for Duchenne and Becker muscular dystrophy gene therapy.

25 September 2018

1 reference

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Physiological correction of Pompe disease by systemic delivery of adeno-associated virus serotype 1 vectors

25 September 2018

1 reference

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Sustained whole-body functional rescue in congestive heart failure and muscular dystrophy hamsters by systemic gene transfer

25 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3253371

Sustained correction of glycogen storage disease type II using adeno-associated virus serotype 1 vectors

25 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3253371

A facile nonviral method for delivering genes and siRNAs to skeletal muscle of mammalian limbs

25 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3253371

Sex significantly influences transduction of murine liver by recombinant adeno-associated viral vectors through an androgen-dependent pathway

25 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3253371

Limb–girdle muscular dystrophies

25 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3253371

10.1007/978-1-61737-982-6_9

15 November 2018

Identifiers

DOI

1 reference

9 August 2017

1 reference

9 August 2017

1 reference