(Q36025267)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26338094%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

title

Efficacy and safety of patisiran for familial amyloidotic polyneuropathy: a phase II multi-dose study (English)

1 reference

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23 February 2020

1

1 reference

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23 February 2020

Isabel Conceição

5

1 reference

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23 February 2020

Hartmut H-J Schmidt

7

1 reference

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23 February 2020

David Adams

13

1 reference

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23 February 2020

author name string

Teresa Coelho

2

1 reference

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23 February 2020

Juan Buades

3

1 reference

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23 February 2020

Jean Pouget

4

1 reference

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23 February 2020

John Berk

6

1 reference

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23 February 2020

Márcia Waddington-Cruz

8

1 reference

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23 February 2020

Josep M Campistol

9

1 reference

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23 February 2020

Brian R Bettencourt

10

1 reference

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23 February 2020

Akshay Vaishnaw

11

1 reference

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23 February 2020

Jared Gollob

12

1 reference

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23 February 2020

publication date

4 September 2015

1 reference

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Orphanet Journal of Rare Diseases

23 February 2020

published in

1 reference

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23 February 2020

volume

10

1 reference

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23 February 2020

page(s)

109

1 reference

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https://scigraph.springernature.com/pub.10.1186/s13023-015-0326-6

23 February 2020

exact match

0 references

cites work

Liver Transplantation for Hereditary Transthyretin Amyloidosis: After 20 Years Still the Best Therapeutic Alternative?

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Rapid progression of familial amyloidotic polyneuropathy: a multinational natural history study

2 October 2017

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Repurposing diflunisal for familial amyloid polyneuropathy: a randomized clinical trial

2 October 2017

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Effect of an RNA interference drug on the synthesis of proprotein convertase subtilisin/kexin type 9 (PCSK9) and the concentration of serum LDL cholesterol in healthy volunteers: a randomised, single-blind, placebo-controlled, phase 1 trial

2 October 2017

1 reference

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Long-term effects of tafamidis for the treatment of transthyretin familial amyloid polyneuropathy

2 October 2017

1 reference

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Tafamidis for transthyretin familial amyloid polyneuropathy: a randomized, controlled trial

2 October 2017

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Activation of complement by therapeutic liposomes and other lipid excipient-based therapeutic products: prediction and prevention

2 October 2017

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Targeted delivery of RNAi therapeutics with endogenous and exogenous ligand-based mechanisms

2 October 2017

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Therapeutic RNAi targeting PCSK9 acutely lowers plasma cholesterol in rodents and LDL cholesterol in nonhuman primates

2 October 2017

1 reference

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Natural history and outcome in systemic AA amyloidosis

2 October 2017

1 reference

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Transthyretin and familial amyloidotic polyneuropathy. Recent progress in understanding the molecular mechanism of neurodegeneration

2 October 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4559363

Outcome in systemic AL amyloidosis in relation to changes in concentration of circulating free immunoglobulin light chains following chemotherapy

2 October 2017

1 reference

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Duplexes of 21-nucleotide RNAs mediate RNA interference in cultured mammalian cells

2 October 2017

1 reference

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Leukocytosis: basics of clinical assessment.

2 October 2017

1 reference

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Potent and specific genetic interference by double-stranded RNA in Caenorhabditis elegans

2 October 2017

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2 October 2017

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Fibril in senile systemic amyloidosis is derived from normal transthyretin

2 October 2017

1 reference

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Progression of transthyretin amyloid neuropathy after liver transplantation

2 October 2017

1 reference

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Safety and efficacy of RNAi therapy for transthyretin amyloidosis

11 July 2018

1 reference

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Effect on disability and safety of Tafamidis in late onset of Met30 transthyretin familial amyloid polyneuropathy.

23 September 2018

1 reference

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Long-term survival after liver transplantation in patients with familial amyloid polyneuropathy.

23 September 2018

1 reference

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RNAi-mediated gene silencing in non-human primates.

23 September 2018

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Contribution of wild-type transthyretin to hereditary peripheral nerve amyloid

23 September 2018

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Liver transplantation for familial amyloidotic polyneuropathy: Impact on Swedish patients' survival

23 September 2018

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Cardiac amyloidosis in African Americans: Comparison of clinical and laboratory features of transthyretin V122I amyloidosis and immunoglobulin light chain amyloidosis

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The course and prognostic factors of familial amyloid polyneuropathy after liver transplantation

21 January 2018

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12 December 2020

Biochemical effect of liver transplantation in two Swedish patients with familial amyloidotic polyneuropathy (FAP-met30)

1 reference

12 December 2020

Progressive cardiac amyloidosis following liver transplantation for familial amyloid polyneuropathy: implications for amyloid fibrillogenesis

1 reference

12 December 2020

Progressive wild-type transthyretin deposition after liver transplantation preferentially occurs onto myocardium in FAP patients

1 reference

12 December 2020

10.1186/S13023-015-0326-6

Identifiers

DOI

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26338094%20AND%20SRC:MED&resulttype=core&format=json

Dimensions Publication ID

23 February 2020

0 references

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26338094%20AND%20SRC:MED&resulttype=core&format=json

23 February 2020

1 reference

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