(Q36968842)

17 August 2017

From the smallest virus to the biggest gene: marching towards gene therapy for duchenne muscular dystrophy (English)

1 reference

17 August 2017

0 references

Dongsheng Duan

1

1 reference

17 August 2017

1 June 2006

1 reference

17 August 2017

1 reference

17 August 2017

6

1 reference

17 August 2017

33

1 reference

17 August 2017

103-108

1 reference

rAAV6-microdystrophin preserves muscle function and extends lifespan in severely dystrophic mice.

17 August 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2581715

C-terminal-truncated microdystrophin recruits dystrobrevin and syntrophin to the dystrophin-associated glycoprotein complex and reduces muscular dystrophy in symptomatic utrophin/dystrophin double-knockout mice

29 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2581715

Efficient in vivo gene expression by trans-splicing adeno-associated viral vectors

29 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2581715

2004 William Allan Award address. Cloning of the DMD gene

29 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2581715

ADENOVIRUS-ASSOCIATED DEFECTIVE VIRUS PARTICLES

29 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2581715

Very mild muscular dystrophy associated with the deletion of 46% of dystrophin

29 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2581715

Modular flexibility of dystrophin: implications for gene therapy of Duchenne muscular dystrophy

29 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2581715

4 September 2018

Identifiers

PMC publication ID

2581715

1 reference

PMC publication ID

2581715

17 August 2017

PubMed publication ID

17234143

1 reference

PMC publication ID

2581715