(Q37001431)

17 August 2017

Complete correction of hemophilia A with adeno-associated viral vectors containing a full-size expression cassette (English)

1 reference

17 August 2017

0 references

0 references

Hui Lu

1

1 reference

17 August 2017

Lingxia Chen

2

1 reference

17 August 2017

Jinhui Wang

3

1 reference

17 August 2017

Bernd Huack

4

1 reference

17 August 2017

Rita Sarkar

5

1 reference

17 August 2017

Shangzhen Zhou

6

1 reference

17 August 2017

Ray Xu

7

1 reference

17 August 2017

Qiulan Ding

8

1 reference

17 August 2017

Xuefeng Wang

9

1 reference

17 August 2017

Hongli Wang

10

1 reference

17 August 2017

Weidong Xiao

11

1 reference

17 August 2017

1 June 2008

1 reference

17 August 2017

1 reference

17 August 2017

19

1 reference

17 August 2017

6

1 reference

17 August 2017

648-654

1 reference

The enhancing effects of the light chain on heavy chain secretion in split delivery of factor VIII gene

17 August 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2596974

Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response

29 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2596974

29 September 2017

Hydrodynamic delivery

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2596974

Packaging capacity of adeno-associated virus serotypes: impact of larger genomes on infectivity and postentry steps

29 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2596974

Adeno-associated virus: a ubiquitous commensal of mammals

29 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2596974

Clades of Adeno-associated viruses are widely disseminated in human tissues.

29 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2596974

High-titer, wild-type free recombinant adeno-associated virus vector production using intron-containing helper plasmids

29 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2596974

Trans-splicing vectors expand the utility of adeno-associated virus for gene therapy

29 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2596974

Advances toward gene therapy for hemophilia at the millennium

29 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2596974

Gene therapy for the hemophilias

29 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2596974

Gene therapy vectors based on adeno-associated virus type 1.

29 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2596974

Biosynthesis, assembly and secretion of coagulation factor VIII.

29 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2596974

Nucleotide sequence and organization of the adeno-associated virus 2 genome

29 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2596974

Quantitative analysis of the packaging capacity of recombinant adeno-associated virus

29 September 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2596974

Self-complementary recombinant adeno-associated viral vectors: packaging capacity and the role of rep proteins in vector purity.

27 June 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2596974

Multiyear therapeutic benefit of AAV serotypes 2, 6, and 8 delivering factor VIII to hemophilia A mice and dogs

4 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2596974

Total correction of hemophilia A mice with canine FVIII using an AAV 8 serotype.

4 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2596974

Phenotypic correction of a mouse model of hemophilia A using AAV2 vectors encoding the heavy and light chains of FVIII.

4 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2596974

A single adeno-associated virus (AAV)-murine factor VIII vector partially corrects the hemophilia A phenotype

4 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2596974

Generation and characterization of chimeric recombinant AAV vectors

4 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2596974

Expanding AAV packaging capacity with trans-splicing or overlapping vectors: a quantitative comparison

4 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2596974

Overcoming adeno-associated virus vector size limitation through viral DNA heterodimerization

4 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2596974

Increasing the size of rAAV-mediated expression cassettes in vivo by intermolecular joining of two complementary vectors

4 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2596974

4 September 2018

Identifiers

DOI

10.1089/HUM.2007.0182

1 reference

17 August 2017

1 reference

17 August 2017

1 reference