(Q37449924)
Statements
Correction in trans for Fabry disease: expression, secretion and uptake of alpha-galactosidase A in patient-derived cells driven by a high-titer recombinant retroviral vector (English)
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Medin JA
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Tudor M
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Simovitch R
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Quirk JM
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Jacobson S
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Murray GJ
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Brady RO
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Identifiers
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