(Q39666591)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20716181%20AND%20SRC:MED&resulttype=core&format=json

10 February 2020

title

Adeno-associated virus gene transfer in Morquio A disease - effect of promoters and sulfatase-modifying factor 1 (English)

1 reference

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10 February 2020

author

Carlos J Alméciga-Díaz

1

1 reference

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10 February 2020

author name string

Adriana M Montaño

2

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20716181%20AND%20SRC:MED&resulttype=core&format=json

10 February 2020

Shunji Tomatsu

3

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20716181%20AND%20SRC:MED&resulttype=core&format=json

10 February 2020

Luis A Barrera

4

1 reference

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10 February 2020

language of work or name

English

0 references

publication date

1 September 2010

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10 February 2020

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20716181%20AND%20SRC:MED&resulttype=core&format=json

10 February 2020

volume

277

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20716181%20AND%20SRC:MED&resulttype=core&format=json

10 February 2020

issue

17

1 reference

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10 February 2020

page(s)

3608-3619

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:20716181%20AND%20SRC:MED&resulttype=core&format=json

International Morquio A Registry: clinical manifestation and natural course of Morquio A disease.

10 February 2020

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AAV1 mediated co-expression of formylglycine-generating enzyme and arylsulfatase a efficiently corrects sulfatide storage in a mouse model of metachromatic leukodystrophy

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Various cells retrovirally transduced with N-acetylgalactosoamine-6-sulfate sulfatase correct Morquio skin fibroblasts in vitro

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Transcriptional silencing is associated with extensive methylation of the CMV promoter following adenoviral gene delivery to muscle

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Delivering multiple gene products in the brain from a single adeno-associated virus vector

21 January 2018

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21 January 2018

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A combined therapeutic approach for pyruvate dehydrogenase deficiency using self-complementary adeno-associated virus serotype-specific vectors and dichloroacetate

21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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Expression in blood cells may contribute to biochemical and pathological improvements after neonatal intravenous gene therapy for mucopolysaccharidosis VII in dogs

21 January 2018

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Sustained phenotypic correction of hemophilia B dogs with a factor IX null mutation by liver-directed gene therapy

21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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Correction of Hunter syndrome in the MPSII mouse model by AAV2/8-mediated gene delivery

21 January 2018

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Neonatal retroviral vector-mediated hepatic gene therapy reduces bone, joint, and cartilage disease in mucopolysaccharidosis VII mice and dogs

21 January 2018

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Analysis of AAV serotypes 1-9 mediated gene expression and tropism in mice after systemic injection

21 January 2018

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21 January 2018

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Recombinant adeno-associated virus purification using novel methods improves infectious titer and yield

21 January 2018

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Quantification of adeno-associated virus particles and empty capsids by optical density measurement

21 January 2018

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Mouse model of N-acetylgalactosamine-6-sulfate sulfatase deficiency (Galns-/-) produced by targeted disruption of the gene defective in Morquio A disease

21 January 2018

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