(Q40619728)

22 September 2017

Improvement of skeletal lesions in mice with mucopolysaccharidosis type VII by neonatal adenoviral gene transfer (English)

1 reference

22 September 2017

Improvement of skeletal lesions in mice with mucopolysaccharidosis type vii by neonatal adenoviral gene transfer (English)

1 reference

https://api.crossref.org/works/10.1016/J.YMTHE.2003.07.004

28 March 2024

1 reference

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A14599804

28 March 2024

1 reference

https://api.crossref.org/works/10.1016/J.YMTHE.2003.07.004

28 March 2024

1 reference

https://api.crossref.org/works/10.1016/J.YMTHE.2003.07.004

28 March 2024

1 reference

https://api.crossref.org/works/10.1016/J.YMTHE.2003.07.004

28 March 2024

author name string

Arihiko Kanaji

1

1 reference

22 September 2017

Motomichi Kosuga

2

1 reference

22 September 2017

Xiao Kang Li

3

1 reference

22 September 2017

Yasuyuki Fukuhara

4

1 reference

22 September 2017

Akiko Tanabe

5

1 reference

22 September 2017

Yuko Kamata

6

1 reference

22 September 2017

Noriyuki Azuma

7

1 reference

22 September 2017

Masao Yamada

8

1 reference

22 September 2017

Toyonori Sakamaki

9

1 reference

22 September 2017

Yoshiaki Toyama

10

1 reference

22 September 2017

Torayuki Okuyama

11

1 reference

22 September 2017

language of work or name

English

1 reference

National Center for Biotechnology Information

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/esummary.fcgi?db=pubmed&retmode=json&id=14599804

28 March 2024

publication date

1 November 2003

1 reference

full work available at URL

22 September 2017

https://doi.org/10.1016/j.ymthe.2003.07.004

online access status

open access

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A14599804

https://api.elsevier.com/content/article/PII:S1525001603002624?httpAccept=text/xml

28 March 2024

1 reference

https://api.crossref.org/works/10.1016/J.YMTHE.2003.07.004

https://api.elsevier.com/content/article/PII:S1525001603002624?httpAccept=text/plain

28 March 2024

1 reference

https://api.crossref.org/works/10.1016/J.YMTHE.2003.07.004

28 March 2024

1 reference

22 September 2017

8

1 reference

22 September 2017

718-725

1 reference

22 September 2017

5

1 reference

Beta glucuronidase deficiency: report of clinical, radiologic, and biochemical features of a new mucopolysaccharidosis

22 September 2017

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Murine mucopolysaccharidosis type VII. Characterization of a mouse with beta-glucuronidase deficiency

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

A single-base-pair deletion in the beta-glucuronidase gene accounts for the phenotype of murine mucopolysaccharidosis type VII

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Gene therapy for murine mucopolysaccharidosis type VII.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Enzyme replacement therapy for murine mucopolysaccharidosis type VII

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Murine mucopolysaccharidosis type VII: long term therapeutic effects of enzyme replacement and enzyme replacement followed by bone marrow transplantation

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Enzyme replacement in murine mucopolysaccharidosis type VII: neuronal and glial response to beta-glucuronidase requires early initiation of enzyme replacement therapy.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Enzyme replacement therapy for murine mucopolysaccharidosis type VII leads to improvements in behavior and auditory function

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Delivery of a retroviral vector expressing human beta-glucuronidase to the liver and spleen decreases lysosomal storage in mucopolysaccharidosis VII mice

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Decreased lysosomal storage in the adult MPS VII mouse brain in the vicinity of grafts of retroviral vector-corrected fibroblasts secreting high levels of beta-glucuronidase

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Cross-correction of beta-glucuronidase deficiency by retroviral vector-mediated gene transfer

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Correction of lysosomal storage in the liver and spleen of MPS VII mice by implantation of genetically modified skin fibroblasts

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Long-term secretion of therapeutic proteins from genetically modified skeletal muscles

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Therapeutic neonatal hepatic gene therapy in mucopolysaccharidosis VII dogs

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Significantly increased expression of beta-glucuronidase in the central nervous system of mucopolysaccharidosis type VII mice from the latency-associated transcript promoter in a nonpathogenic herpes simplex virus type 1 vector

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Herpesvirus vector gene transfer and expression of beta-glucuronidase in the central nervous system of MPS VII mice

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Extensive beta-glucuronidase activity in murine central nervous system after adenovirus-mediated gene transfer to brain.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Adenovirus-mediated gene transfer and expression of human beta-glucuronidase gene in the liver, spleen, and central nervous system in mucopolysaccharidosis type VII mice

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Engraftment of genetically engineered amniotic epithelial cells corrects lysosomal storage in multiple areas of the brain in mucopolysaccharidosis type VII mice

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Adenovirus-mediated gene therapy for mucopolysaccharidosis VII: involvement of cross-correction in wide-spread distribution of the gene products and long-term effects of CTLA-4Ig coexpression

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Adenovirus-mediated gene therapy for corneal clouding in mice with mucopolysaccharidosis type VII.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Long-term normalization in the central nervous system, ocular manifestations, and skeletal deformities by a single systemic adenovirus injection into neonatal mice with mucopolysaccharidosis VII.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

In vivo treatment of hemophilia A and mucopolysaccharidosis type VII using nonprimate lentiviral vectors.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Reversal of pathology in the entire brain of mucopolysaccharidosis type VII mice after lentivirus-mediated gene transfer.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Recombinant adeno-associated virus-mediated correction of lysosomal storage within the central nervous system of the adult mucopolysaccharidosis type VII mouse

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Neonatal intramuscular injection with recombinant adeno-associated virus results in prolonged beta-glucuronidase expression in situ and correction of liver pathology in mucopolysaccharidosis type VII mice.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Neonatal gene transfer leads to widespread correction of pathology in a murine model of lysosomal storage disease.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Prevention of systemic clinical disease in MPS VII mice following AAV-mediated neonatal gene transfer

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Mucopolysaccharidosis VII in a cat.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Growth plate pathology in feline mucopolysaccharidosis VI

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Articular chondrocytes from animals with a dermatan sulfate storage disease undergo a high rate of apoptosis and release nitric oxide and inflammatory cytokines: a possible mechanism underlying degenerative joint disease in the mucopolysaccharidoses

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Adeno-associated virus mediates long-term gene transfer and delivery of chondroprotective IL-4 to murine synovium.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

In vivo gene delivery to synovium by lentiviral vectors.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

Phenotype correction in murine mucopolysaccharidosis type VII by transplantation of human amniotic epithelial cells after adenovirus-mediated gene transfer

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2003.07.004

inferred from DOI database lookup

7 January 2021

based on heuristic

Identifiers

1 reference

22 September 2017

1 reference