(Q41207261)

28 September 2017

title

Clinical application of somatic gene therapy in inborn errors of metabolism (English)

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28 September 2017

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F D Ledley

1

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28 September 2017

publication date

1 January 1990

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Journal of Inherited Metabolic Disease

28 September 2017

published in

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28 September 2017

volume

13

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28 September 2017

issue

4

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28 September 2017

page(s)

597-616

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Human gene therapy: scientific and ethical considerations

28 September 2017

cites work

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Crossref

https://api.crossref.org/works/10.1007%2FBF01799515

Expression of human adenosine deaminase in murine hematopoietic cells

21 January 2018

1 reference

Crossref

https://api.crossref.org/works/10.1007%2FBF01799515

Ethical issues in and beyond prospective clinical trials of human gene therapy

21 January 2018

1 reference

Crossref

https://api.crossref.org/works/10.1007%2FBF01799515

Expression of an exogenous growth hormone gene by transplantable human epidermal cells

21 January 2018

1 reference

12 December 2020

Replacement of liver function in rats by transplantation of microcarrier-attached hepatocytes

1 reference

12 December 2020

Behavioral and neurochemical evaluation of a transgenic mouse model of Lesch-Nyhan syndrome.

1 reference

12 December 2020

Treatment of enzyme deficiency by hepatocyte transplantation in rats

1 reference

12 December 2020

Grafting genetically modified cells to the damaged brain: restorative effects of NGF expression

1 reference

12 December 2020

Self-inactivating retroviral vectors designed for transfer of whole genes into mammalian cells

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12 December 2020

Introduction of a selectable gene into primitive stem cells capable of long-term reconstitution of the hemopoietic system of W/Wv mice.

1 reference

12 December 2020

Cellular transplantation in the treatment of experimental hepatic failure

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12 December 2020

Gene expression from transcriptionally disabled retroviral vectors

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12 December 2020

High efficiency transformation by direct microinjection of DNA into cultured mammalian cells

1 reference

12 December 2020

Generation of cDNA probes directed by amino acid sequence: cloning of urate oxidase

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12 December 2020

Somatic gene therapy for human disease: a problem of eugenics?

1 reference

12 December 2020

Unsuccessful trial of gene replacement in arginase deficiency

1 reference

12 December 2020

Mevinolin, an inhibitor of cholesterol synthesis, induces mRNA for low density lipoprotein receptor in livers of hamsters and rabbits

1 reference

12 December 2020

Gene therapy for human genetic disease?

1 reference

12 December 2020

Phenylketonuria; a problem in eugenics

1 reference

12 December 2020

Induction of arginase activity with the Shope papilloma virus in tissue culture cells from an argininemic patient

1 reference

12 December 2020

Correction of the genetic defect in hepatocytes from the Watanabe heritable hyperlipidemic rabbit.

1 reference

12 December 2020

Germ line transmission and expression of a corrected HPRT gene produced by gene targeting in embryonic stem cells

1 reference

12 December 2020

Treatment of type 1 diabetes mellitus in non-obese diabetic mice by transplantation of allogeneic bone marrow and pancreatic tissue

1 reference

12 December 2020

Induction of an enzyme in genetically deficient rats after grafting of normal liver.

1 reference

12 December 2020

New method of hepatocyte transplantation and extracorporeal liver support

1 reference

12 December 2020

Retrovirus-mediated transfer of the human glucocerebrosidase gene to Gaucher fibroblasts

1 reference

12 December 2020

Electroporation for the efficient transfection of mammalian cells with DNA.

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12 December 2020

Selection for phenylalanine hydroxylase activity in cells transformed with recombinant retroviruses

1 reference

12 December 2020

Retroviral-mediated gene transfer and expression of human phenylalanine hydroxylase in primary mouse hepatocytes

1 reference

12 December 2020

Effect of viable isolated hepatocytes or hepatocyte fractions on survival rate following galactosamine-induced acute liver failure

1 reference

12 December 2020

1 reference

12 December 2020

Survival, organization, and function of microcarrier-attached hepatocytes transplanted in rats

1 reference

12 December 2020

Efficient retrovirus-mediated transfer and expression of a human adenosine deaminase gene in diploid skin fibroblasts from an adenosine deaminase-deficient human

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12 December 2020

Recombinant gene expression in vivo within endothelial cells of the arterial wall

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12 December 2020

Phenylketonuria: epitome of human biochemical genetics (first of two parts).

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12 December 2020

Retroviral gene transfer into primary hepatocytes: implications for genetic therapy of liver-specific functions

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12 December 2020

Transplantation of Hepatocytes for Treatment of Surgically Induced Acute Hepatic Failure in the Rat

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12 December 2020

Biopsy of human preimplantation embryos and sexing by DNA amplification.

1 reference

12 December 2020

Liver transplantation, including the concept of reduced-size liver transplants in children

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12 December 2020

Somatic gene therapy. Current status and future prospects

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12 December 2020

Expression of a foreign gene in myeloid and lymphoid cells derived from multipotent haematopoietic precursors.

1 reference

12 December 2020

Treatment of episodic hyperammonemia in children with inborn errors of urea synthesis

1 reference

12 December 2020

Studies on ectopic liver utilizing hepatocyte transplantation into the rat spleen

1 reference

12 December 2020

Somatic gene therapy for human disease: background and prospects. Part I.

1 reference

12 December 2020

Hepatocellular transplantation in acute liver failure

1 reference

12 December 2020

Extracorporeal enzyme reactors for depletion of phenylalanine in phenylketonuria

1 reference

12 December 2020

Gene expression in implanted rat hepatocytes following retroviral-mediated gene transfer.

1 reference

12 December 2020

Canine model for gene therapy: inefficient gene expression in dogs reconstituted with autologous marrow infected with retroviral vectors

1 reference

12 December 2020

Lineage-specific expression of a human beta-globin gene in murine bone marrow transplant recipients reconstituted with retrovirus-transduced stem cells

1 reference

12 December 2020

The application of bone marrow transplantation to the treatment of genetic diseases

1 reference

12 December 2020

Adult mammalian hepatocyte as target cell for retroviral gene transfer: a model for gene therapy

1 reference

12 December 2020

Effects of partial hepatectomy on transplanted hepatocytes

1 reference

12 December 2020

Prospects for Human Gene Therapy

1 reference

12 December 2020

Effects of intrasplenic injection of hepatocytes, hepatocyte fragments and hepatocyte culture supernatants on D-galactosamine-induced liver failure in rats

1 reference

12 December 2020

Hepatocellular transplantation in rats with toxic induced liver failure: results of iso-, allo- and xenografts

1 reference

12 December 2020

Bone marrow transplantation in Lesch-Nyhan disease

1 reference

12 December 2020

Insertion of DNA sequences into the human chromosomal beta-globin locus by homologous recombination

1 reference

12 December 2020

Tissue-specific expression of the human alpha 1-antitrypsin gene is controlled by multiple cis-regulatory elements

1 reference

12 December 2020

Mechanisms and applications of DNA-mediated gene transfer in mammalian cells — a review

1 reference

12 December 2020

Retrovirus-mediated transduction of adult hepatocytes

1 reference

12 December 2020

Sounding boards. Gene therapy in human beings: when is it ethical to begin?

1 reference

12 December 2020

Construction of a retrovirus packaging mutant and its use to produce helper-free defective retrovirus

1 reference

12 December 2020

Complete correction of the enzymatic defect of type I Gaucher disease fibroblasts by retroviral-mediated gene transfer

1 reference

12 December 2020

Homocystinuria--the effects of betaine in the treatment of patients not responsive to pyridoxine.

1 reference

12 December 2020

Correction of hyperbilirubinemia in the glucuronyltransferase-deficient rat by intraportal hepatocyte transplantation

1 reference

12 December 2020

Grafting genetically modified cells to the brain: possibilities for the future

1 reference

12 December 2020

Displacement bone marrow transplantation for some inborn errors

1 reference

12 December 2020

Site-directed mutagenesis by gene targeting in mouse embryo-derived stem cells

1 reference

12 December 2020

Open microsurgical autograft of adrenal medulla to the right caudate nucleus in two patients with intractable Parkinson's disease.

1 reference

12 December 2020

Hepatocellular transplantation for metabolic deficiencies: decrease of plasms bilirubin in Gunn rats

1 reference

12 December 2020

Site-directed neovessel formation in vivo

1 reference

12 December 2020

Implantation of vascular grafts lined with genetically modified endothelial cells

1 reference

12 December 2020

A new technique for the assay of infectivity of human adenovirus 5 DNA

1 reference

12 December 2020

Expression of retrovirally transduced genes in primary cultures of adult rat hepatocytes

1 reference

12 December 2020

Expression of human adenosine deaminase in nonhuman primates after retrovirus-mediated gene transfer

1 reference

12 December 2020

Targetted correction of a mutant HPRT gene in mouse embryonic stem cells

1 reference

12 December 2020

A safe packaging line for gene transfer: separating viral genes on two different plasmids

1 reference

12 December 2020

Identifiers

DOI

10.1007/BF01799515

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Dimensions Publication ID

28 September 2017

1016971648

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