(Q41625113)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:9348647%20AND%20SRC:MED&resulttype=core&format=json

7 November 2019

review article

1 reference

title

Gene therapy of Duchenne muscular dystrophy (English)

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:9348647%20AND%20SRC:MED&resulttype=core&format=json

7 November 2019

0 references

A Fassati

1

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:9348647%20AND%20SRC:MED&resulttype=core&format=json

7 November 2019

S Murphy

series ordinal

2

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:9348647%20AND%20SRC:MED&resulttype=core&format=json

7 November 2019

G Dickson

series ordinal

3

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:9348647%20AND%20SRC:MED&resulttype=core&format=json

7 November 2019

publication date

1 January 1997

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:9348647%20AND%20SRC:MED&resulttype=core&format=json

7 November 2019

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:9348647%20AND%20SRC:MED&resulttype=core&format=json

7 November 2019

volume

35

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:9348647%20AND%20SRC:MED&resulttype=core&format=json

7 November 2019

page(s)

117-153

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:9348647%20AND%20SRC:MED&resulttype=core&format=json

Accurate assessment of intragenic recombination frequency within the Duchenne muscular dystrophy gene

7 November 2019

cites work

1 reference

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7 January 2021

Human dystrophin expression in mdx mice after intramuscular injection of DNA constructs

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7 January 2021

Adenovirus-mediated gene transfer into striated muscles.

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7 January 2021

The structural and functional diversity of dystrophin

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7 January 2021

Syntrophin binds to an alternatively spliced exon of dystrophin

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7 January 2021

Transfer of a foreign gene into the brain using adenovirus vectors

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7 January 2021

Expression of a recombinant dystrophin in mdx mice using adenovirus vector

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7 January 2021

Skeletal muscle regeneration

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7 January 2021

Cellular Aspect of Muscle Growth: Myogenic Cell Proliferation

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7 January 2021

Non-invasive liposome-mediated gene delivery can correct the ion transport defect in cystic fibrosis mutant mice

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7 January 2021

Functional regeneration in the hindlimb skeletal muscle of the mdx mouse

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7 January 2021

Serial position memory of boys with Duchenne muscular dystrophy

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7 January 2021

Clinical-molecular correlation in 104 mild X-linked muscular dystrophy patients: characterization of sub-clinical phenotypes

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7 January 2021

Immunostaining of skeletal and cardiac muscle surface membrane with antibody against Duchenne muscular dystrophy peptide

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7 January 2021

Mosaic expression of dystrophin in symptomatic carriers of Duchenne's muscular dystrophy

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7 January 2021

Specificity of expression of the muscle and brain dystrophin gene promoters in muscle and brain cells

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7 January 2021

Systemic delivery of recombinant proteins by genetically modified myoblasts

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7 January 2021

[A new x-chromosomal muscular dystrophy]

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7 January 2021

An efficient and flexible system for construction of adenovirus vectors with insertions or deletions in early regions 1 and 3.

1 reference

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7 January 2021

Cognitive functions in Duchenne muscular dystrophy: a reappraisal and comparison with spinal muscular atrophy

1 reference

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7 January 2021

Duchenne muscular dystrophy: deficiency of dystrophin at the muscle cell surface

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7 January 2021

Dystrophin is transcribed in brain from a distant upstream promoter.

1 reference

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7 January 2021

X chromosome-linked muscular dystrophy (mdx) in the mouse

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7 January 2021

An alternative dystrophin transcript specific to peripheral nerve

1 reference

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7 January 2021

Three muscular dystrophies: loss of cytoskeleton-extracellular matrix linkage.

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Muscular dystrophy in the mdx mouse: histopathology of the soleus and extensor digitorum longus muscles.

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Duchenne muscular dystrophy: plasma membrane loss initiates muscle cell necrosis unless it is repaired

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Dystrophin is localized to the plasma membrane of human skeletal muscle fibers by electron-microscopic cytochemical study

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Regional localization of the murine Duchenne muscular dystrophy gene on the mouse X chromosome

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Expression of the murine Duchenne muscular dystrophy gene in muscle and brain

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Transcription of the dystrophin gene in human muscle and non-muscle tissue

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

A G+1-->A transversion at the 5' splice site of intron 69 of the dystrophin gene causing the absence of peripheral nerve Dp116 and severe clinical involvement in a DMD patient.

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

The homologue of the Duchenne locus is defective in X-linked muscular dystrophy of dogs

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Deletion analysis of the dystrophin-actin binding domain

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Overexpression of dystrophin in transgenic mdx mice eliminates dystrophic symptoms without toxicity

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

New mdx mutation disrupts expression of muscle and nonmuscle isoforms of dystrophin

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Dp71 can restore the dystrophin-associated glycoprotein complex in muscle but fails to prevent dystrophy.

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Structural predictions for the central domain of dystrophin

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Gene therapy via primary myoblasts: long-term expression of factor IX protein following transplantation in vivo

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Dystrophin expression improves myofiber survival in mdx muscle following intramuscular plasmid DNA injection.

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Plasmid DNA is superior to viral vectors for direct gene transfer into adult mouse skeletal muscle

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Direct gene transfer into mouse diaphragm

1 reference

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7 January 2021

Direct gene transfer into skeletal muscle in vivo: factors affecting efficiency of transfer and stability of expression

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7 January 2021

Systemic delivery of human growth hormone by injection of genetically engineered myoblasts.

1 reference

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7 January 2021

Human dystrophin gene transfer: production and expression of a functional recombinant DNA-based gene

1 reference

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7 January 2021

Retroviral-mediated transfer of a dystrophin minigene into mdx mouse myoblasts in vitro

1 reference

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7 January 2021

Direct retroviral-mediated transfer of a dystrophin minigene into mdx mouse muscle in vivo

1 reference

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7 January 2021

Differential expression of muscular dystrophy in diaphragm versus hindlimb muscles of mdx mice

1 reference

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7 January 2021

Development of apposed sarcoplasmic reticulum at the T system and sarcolemma and the change in orientation of triads in rat skeletal muscle

1 reference

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7 January 2021

Very mild muscular dystrophy associated with the deletion of 46% of dystrophin

1 reference

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7 January 2021

Membrane organization of the dystrophin-glycoprotein complex

1 reference

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7 January 2021

A role for the dystrophin-glycoprotein complex as a transmembrane linker between laminin and actin.

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Efficiency of in vivo gene transfer using murine retroviral vectors is strain-dependent in mice

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Transplantation of retroviral producer cells for in vivo gene transfer into mouse skeletal muscle

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Alternative splicing of human dystrophin mRNA generates isoforms at the carboxy terminus

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Lipofection: a highly efficient, lipid-mediated DNA-transfection procedure

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

A retroviral vector containing a muscle-specific enhancer drives gene expression only in differentiated muscle fibers

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Virus proteins that counteract host immune defenses

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Expression of four alternative dystrophin transcripts in brain regions regulated by different promoters.

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Characteristics of a human cell line transformed by DNA from human adenovirus type 5

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Exogenous Dp71 restores the levels of dystrophin associated proteins but does not alleviate muscle damage in mdx mice

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Analysis of the actin-binding domain of alpha-actinin by mutagenesis and demonstration that dystrophin contains a functionally homologous domain

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Dystrophinopathy in isolated cases of myopathy in females

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Dystrophin: the protein product of the Duchenne muscular dystrophy locus

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Characterization of dystrophin in muscle-biopsy specimens from patients with Duchenne's or Becker's muscular dystrophy

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Gene transfer into skeletal muscles by isogenic myoblasts

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Distal transcript of the dystrophin gene initiated from an alternative first exon and encoding a 75-kDa protein widely distributed in nonmuscle tissues

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Primary structure of dystrophin-associated glycoproteins linking dystrophin to the extracellular matrix

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Brain morphology in Duchenne muscular dystrophy: a Golgi study

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Direct gene transfer into nonhuman primate myofibers in vivo

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

New Procedure for DNA Transfection with Polycation and Dimethyl Sulfoxide

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Myoblast transfer in Duchenne muscular dystrophy

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Tissue-specific targeting of retroviral vectors through ligand-receptor interactions

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Very efficient myoblast allotransplantation in mice under FK506 immunosuppression

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Molecular and functional analysis of the muscle-specific promoter region of the Duchenne muscular dystrophy gene

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

The complete sequence of dystrophin predicts a rod-shaped cytoskeletal protein

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Anabolic steroid treatment increases myofiber damage in mdx mouse muscular dystrophy

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Adenovirus and adeno-associated virus mediated gene transfer

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Beneficial effects of transplanting normal limb-bud mesenchyme into dystrophic mouse muscles

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Dystrophin production induced by myoblast transfer therapy in Duchenne muscular dystrophy

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

New muscle transplant method produces normal twitch tension in dystrophic muscle

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

A 71-kilodalton protein is a major product of the Duchenne muscular dystrophy gene in brain and other nonmuscle tissues

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

A housekeeping type promoter, located in the 3' region of the Duchenne muscular dystrophy gene, controls the expression of Dp71, a major product of the gene

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

The chicken dystrophin cDNA: striking conservation of the C-terminal coding and 3' untranslated regions between man and chicken

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

The interaction of actin with dystrophin

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Binding sites involved in the interaction of actin with the N-terminal region of dystrophin

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

The distribution of dystrophin in the murine central nervous system: an immunocytochemical study.

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Localization of dystrophin to postsynaptic regions of central nervous system cortical neurons.

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Dp140: a novel 140 kDa CNS transcript from the dystrophin locus

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Developmental Fate of Skeletal Muscle Satellite Cells

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Becker muscular dystrophy patient with a large intragenic dystrophin deletion: implications for functional minigenes and gene therapy

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Brain-type and muscle-type promoters of the dystrophin gene differ greatly in structure

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Construction of a retrovirus packaging mutant and its use to produce helper-free defective retrovirus

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Complement-specific antibodies: Designing novel anti-inflammatories

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Immunohistochemical analysis of dystrophin-associated proteins in Becker/Duchenne muscular dystrophy with huge in-frame deletions in the NH2-terminal and rod domains of dystrophin

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Deficiency of the 50K dystrophin-associated glycoprotein in severe childhood autosomal recessive muscular dystrophy

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Deficiency of dystrophin-associated proteins in Duchenne muscular dystrophy patients lacking COOH-terminal domains of dystrophin

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Cardiac involvement in Becker muscular dystrophy.

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Gene transfer by retrovirus vectors occurs only in cells that are actively replicating at the time of infection

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Cardiomyopathy may be the only clinical manifestation in female carriers of Duchenne muscular dystrophy

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Rescue, propagation, and partial purification of a helper virus-dependent adenovirus vector

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Becker muscular dystrophy with early manifestation of left heart failure

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Duchenne dystrophy: Electron microscopic findings pointing to a basic or early abnormality in the plasma membrane of the muscle fiber

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

An explanation for the phenotypic differences between patients bearing partial deletions of the DMD locus

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Isolation of candidate cDNAs for portions of the Duchenne muscular dystrophy gene

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Growth of Human Striated Muscle

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Partial correction of an inherited biochemical defect of skeletal muscle by grafts of normal muscle precursor cells

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Normal myogenic cells from newborn mice restore normal histology to degenerating muscles of the mdx mouse

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

The relationship between the dimensions of the fibres and the number of nuclei during restricted growth, degrowth and compensatory growth of skeletal muscle

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

The relationship between the dimensions of the fibres and the number of nuclei during normal growth of skeletal muscle in the domestic fowl

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Brief report: deletion of the dystrophin muscle-promoter region associated with X-linked dilated cardiomyopathy.

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Transplantation of adult-derived myoblasts in mice following gene transfer

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Adenovirus entry into host cells: a role for alpha(v) integrins

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

The "rescue" of dystrophin synthesis in boys with Duchenne muscular dystrophy

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Identification of a novel first exon in the human dystrophin gene and of a new promoter located more than 500 kb upstream of the nearest known promoter

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Expression of the putative Duchenne muscular dystrophy gene in differentiated myogenic cell cultures and in the brain

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Two hot spots of recombination in the DMD gene correlate with the deletion prone regions

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Evidence of fusion between host and donor myoblasts in skeletal muscle grafts

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Conversion of mdx myofibres from dystrophin-negative to -positive by injection of normal myoblasts

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Half the dystrophin gene is apparently enough for a mild clinical course: confirmation of its potential use for gene therapy.

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Mechanical function of dystrophin in muscle cells

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Genetic and biochemical normalization in female carriers of Duchenne muscular dystrophy: evidence for failure of dystrophin production in dystrophin-competent myonuclei

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Dystrophin protects the sarcolemma from stresses developed during muscle contraction

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Expression of full-length and truncated dystrophin mini-genes in transgenic mdx mice

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Dilated cardiomyopathy requiring cardiac transplantation as initial manifestation of Xp21 Becker type muscular dystrophy

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Dystrophin expression in the human retina is required for normal function as defined by electroretinography

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Intelligence and the gene for Duchenne muscular dystrophy

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Adenovirus as an expression vector in muscle cells in vivo

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Efficient adenovirus-mediated transfer of a human minidystrophin gene to skeletal muscle of mdx mice

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Point mutations in the dystrophin gene

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Exon structure of the human dystrophin gene

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

The cerebral defect and myopathy in Duchenne muscular dystrophy A comparative clinicopathological study

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Protection of retroviral vector particles in human blood through complement inhibition

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Retroviral vector-mediated gene transfer into human primary myogenic cells leads to expression in muscle fibers in vivo

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Molecular shape of dystrophin

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Non-viral approaches to gene therapy

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

An error in dystrophin mRNA processing in golden retriever muscular dystrophy, an animal homologue of Duchenne muscular dystrophy

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

The molecular basis of muscular dystrophy in the mdx mouse: a point mutation

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Genes transferred by retroviral vectors into normal and mutant myoblasts in primary cultures are expressed in myotubes

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Generation of targeted retroviral vectors by using single-chain variable fragment: an approach to in vivo gene delivery

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

The mdx mouse diaphragm reproduces the degenerative changes of Duchenne muscular dystrophy

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Molecular organization at the glycoprotein-complex-binding site of dystrophin. Three dystrophin-associated proteins bind directly to the carboxy-terminal portion of dystrophin

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Mammalian alpha 1- and beta 1-syntrophin bind to the alternative splice-prone region of the dystrophin COOH terminus

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Glycoprotein-binding site of dystrophin is confined to the cysteine-rich domain and the first half of the carboxy-terminal domain

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Modulation of in vitro splicing of the upstream intron by modifying an intra-exon sequence which is deleted from the dystrophin gene in dystrophin Kobe

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

The human dystrophin gene requires 16 hours to be transcribed and is cotranscriptionally spliced

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Apo-dystrophin-3: a 2.2kb transcript from the DMD locus encoding the dystrophin glycoprotein binding site

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Brain abnormalities in Duchenne muscular dystrophy: phosphorus-31 magnetic resonance spectroscopy and neuropsychological study.

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Results of a triple blind clinical study of myoblast transplantations without immunosuppressive treatment in young boys with Duchenne muscular dystrophy.

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Liposome-mediated gene transfer into normal and dystrophin-deficient mouse myoblasts.

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

PCR and immunoblot analyses of dystrophin in Becker muscular dystrophy

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Intrafamilial variability in dystrophin abundance correlated with difference in the severity of the phenotype

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Canine X-linked muscular dystrophy: morphologic lesions

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Form and Function of Retroviral Proviruses

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Long-term correction of mouse dystrophic degeneration by adenovirus-mediated transfer of a minidystrophin gene

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Gene transfer in regenerating muscle

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Coupling of adenovirus to transferrin-polylysine/DNA complexes greatly enhances receptor-mediated gene delivery and expression of transfected genes

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Dystrophin distribution in heterozygote MDX mice

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Use of mononuclear precursor cells to insert allogeneic genes into growing mouse muscles

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Improved gene transfer by direct plasmid injection associated with regeneration in mouse skeletal muscle.

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Age and sex influence expression of plasmid DNA directly injected into mouse skeletal muscle

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Expression of human full-length and minidystrophin in transgenic mdx mice: implications for gene therapy of Duchenne muscular dystrophy

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Human dystrophin expression corrects the myopathic phenotype in transgenic mdx mice

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Human serum lyses RNA tumour viruses

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Integrins alpha v beta 3 and alpha v beta 5 promote adenovirus internalization but not virus attachment

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Integrins as virus receptors

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Long-term persistence of plasmid DNA and foreign gene expression in mouse muscle

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Direct gene transfer into mouse muscle in vivo

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Muscular dystrophies: diseases of the dystrophin-glycoprotein complex

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Cellular immunity to viral antigens limits E1-deleted adenoviruses for gene therapy

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Inactivation of E2a in recombinant adenoviruses improves the prospect for gene therapy in cystic fibrosis.

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Safety and efficacy of repetitive adenovirus-mediated transfer of CFTR cDNA to airway epithelia of primates and cotton rats.

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Serum creatine-kinase (CK) and pyruvate-kinase (PK) activities in Duchenne (DMD) as compared with Becker (BMD) muscular dystrophy

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Systemic gene expression after intravenous DNA delivery into adult mice

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

A differential efficiency of adenovirus-mediated in vivo gene transfer into skeletal muscle cells of different maturity

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Retroviral retargeting by envelopes expressing an N-terminal binding domain.

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Dystrophin, its gene, and the dystrophinopathies

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

Cellular and humoral immune responses to viral antigens create barriers to lung-directed gene therapy with recombinant adenoviruses

1 reference

https://api.crossref.org/works/10.1016%2FS0065-2660%2808%2960449-6

7 January 2021

10.1016/S0065-2660(08)60449-6

Identifiers

DOI

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:9348647%20AND%20SRC:MED&resulttype=core&format=json

7 November 2019

1 reference