(Q44103069)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:12716937%20AND%20SRC:MED&resulttype=core&format=json

3 November 2019

title

Intravitreal gene therapy reduces lysosomal storage in specific areas of the CNS in mucopolysaccharidosis VII mice (English)

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:12716937%20AND%20SRC:MED&resulttype=core&format=json

3 November 2019

0 references

7

1 reference

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3 November 2019

author name string

Anne K Hennig

1

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:12716937%20AND%20SRC:MED&resulttype=core&format=json

3 November 2019

Beth Levy

2

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:12716937%20AND%20SRC:MED&resulttype=core&format=json

3 November 2019

Judith Mosinger Ogilvie

3

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:12716937%20AND%20SRC:MED&resulttype=core&format=json

3 November 2019

Carole A Vogler

4

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:12716937%20AND%20SRC:MED&resulttype=core&format=json

3 November 2019

Nancy Galvin

5

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:12716937%20AND%20SRC:MED&resulttype=core&format=json

3 November 2019

Steven Bassnett

6

1 reference

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3 November 2019

language of work or name

English

0 references

publication date

1 April 2003

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:12716937%20AND%20SRC:MED&resulttype=core&format=json

3 November 2019

published in

Journal of Neuroscience

1 reference

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3 November 2019

volume

23

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3 November 2019

issue

8

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3 November 2019

page(s)

3302-3307

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:12716937%20AND%20SRC:MED&resulttype=core&format=json

Neonatal intramuscular injection with recombinant adeno-associated virus results in prolonged beta-glucuronidase expression in situ and correction of liver pathology in mucopolysaccharidosis type VII mice.

3 November 2019

cites work

1 reference

12 December 2020

Neonatal gene transfer leads to widespread correction of pathology in a murine model of lysosomal storage disease.

1 reference

12 December 2020

Systemic and central nervous system correction of lysosomal storage in mucopolysaccharidosis type VII mice

1 reference

12 December 2020

Persistent transgene product in retina, optic nerve and brain after intraocular injection of rAAV.

1 reference

12 December 2020

Recombinant adeno-associated virus purification using novel methods improves infectious titer and yield

1 reference

12 December 2020

Sustained production of beta-glucuronidase from localized sites after AAV vector gene transfer results in widespread distribution of enzyme and reversal of lysosomal storage lesions in a large volume of brain in mucopolysaccharidosis VII mice.

1 reference

12 December 2020

Recombinant adeno-associated virus-mediated correction of lysosomal storage within the central nervous system of the adult mucopolysaccharidosis type VII mouse

1 reference

12 December 2020

Reversal of pathology in the entire brain of mucopolysaccharidosis type VII mice after lentivirus-mediated gene transfer.

1 reference

12 December 2020

Retinal function is improved in a murine model of a lysosomal storage disease following bone marrow transplantation

1 reference

12 December 2020

Intracranial injection of recombinant adeno-associated virus improves cognitive function in a murine model of mucopolysaccharidosis type VII.

1 reference

12 December 2020

Prevention of systemic clinical disease in MPS VII mice following AAV-mediated neonatal gene transfer

1 reference

12 December 2020

Neurological correction of lysosomal storage in a mucopolysaccharidosis IIIB mouse model by adeno-associated virus-mediated gene delivery

1 reference

12 December 2020

Functional correction of established central nervous system deficits in an animal model of lysosomal storage disease with feline immunodeficiency virus-based vectors

1 reference

12 December 2020

Distribution of a lysosomal enzyme in the adult brain by axonal transport and by cells of the rostral migratory stream.

1 reference

12 December 2020

Structure and function of the mannose 6-phosphate/insulinlike growth factor II receptors

1 reference

12 December 2020

A murine model of mucopolysaccharidosis VII. Gross and microscopic findings in beta-glucuronidase-deficient mice

1 reference

12 December 2020

Murine mucopolysaccharidosis type VII. Characterization of a mouse with beta-glucuronidase deficiency

1 reference

12 December 2020

Birth dates of retinal ganglion cells giving rise to the crossed and uncrossed optic projections in the mouse

1 reference

12 December 2020

Inborn errors of mucopolysaccharide metabolism

1 reference

12 December 2020

Intracellular transport in neurons

1 reference

12 December 2020

A single-base-pair deletion in the beta-glucuronidase gene accounts for the phenotype of murine mucopolysaccharidosis type VII

1 reference

12 December 2020

Treatment of murine mucopolysaccharidosis type VII by syngeneic bone marrow transplantation in neonates.

1 reference

12 December 2020

Neuropathology of murine mucopolysaccharidosis type VII.

1 reference

12 December 2020

Cellular pathology of lysosomal storage disorders.

1 reference

12 December 2020

Enzyme replacement therapy for murine mucopolysaccharidosis type VII leads to improvements in behavior and auditory function

1 reference

12 December 2020

Recombinant adeno-associated virus vector: use for transgene expression and anterograde tract tracing in the CNS

1 reference

12 December 2020

Murine mucopolysaccharidosis type VII: the impact of therapies on the clinical course and pathology in a murine model of lysosomal storage disease

1 reference

12 December 2020

Extensive beta-glucuronidase activity in murine central nervous system after adenovirus-mediated gene transfer to brain.

1 reference

12 December 2020

10.1523/JNEUROSCI.23-08-03302.2003

Identifiers

DOI

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:12716937%20AND%20SRC:MED&resulttype=core&format=json

3 November 2019

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:12716937%20AND%20SRC:MED&resulttype=core&format=json

3 November 2019

1 reference