(Q45000795)

8 December 2017

title

Hematopoietic stem cell gene therapy of murine protoporphyria by methylguanine-DNA-methyltransferase-mediated in vivo drug selection (English)

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8 December 2017

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E Richard

1

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8 December 2017

E Robert

2

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8 December 2017

M Cario-André

3

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8 December 2017

C Ged

4

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8 December 2017

F Géronimi

5

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8 December 2017

S L Gerson

6

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8 December 2017

H de Verneuil

7

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8 December 2017

F Moreau-Gaudry

8

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8 December 2017

publication date

1 November 2004

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8 December 2017

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8 December 2017

volume

11

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8 December 2017

issue

22

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8 December 2017

page(s)

1638-1647

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https://scigraph.springernature.com/pub.10.1038/sj.gt.3302335

8 December 2017

exact match

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cites work

Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease

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Sustained correction of X-linked severe combined immunodeficiency by ex vivo gene therapy

21 January 2018

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Clonality analysis after retroviral-mediated gene transfer to CD34+ cells from the cord blood of ADA-deficient SCID neonates

21 January 2018

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HIV, but not murine leukemia virus, vectors mediate high efficiency gene transfer into freshly isolated G0/G1 human hematopoietic stem cells

21 January 2018

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https://api.crossref.org/works/10.1038%2FSJ.GT.3302335

Transduction of human CD34+ cells that mediate long-term engraftment of NOD/SCID mice by HIV vectors

21 January 2018

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Stable transduction of quiescent CD34(+)CD38(-) human hematopoietic cells by HIV-1-based lentiviral vectors

21 January 2018

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Human cord blood CD34+CD38- cell transduction via lentivirus-based gene transfer vectors.

21 January 2018

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Development of a novel trans-lentiviral vector that affords predictable safety

21 January 2018

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Advances in lentiviral vector design for gene-modification of hematopoietic stem cells.

21 January 2018

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RNA 3' readthrough of oncoretrovirus and lentivirus: implications for vector safety and efficacy

21 January 2018

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Performance- and safety-enhanced lentiviral vectors containing the human interferon-beta scaffold attachment region and the chicken beta-globin insulator

21 January 2018

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Correction of ADA-SCID by stem cell gene therapy combined with nonmyeloablative conditioning

21 January 2018

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Lentivirus-mediated gene transfer into hematopoietic repopulating cells in baboons.

21 January 2018

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Mechanism of inactivation of human O6-alkylguanine-DNA alkyltransferase by O6-benzylguanine

21 January 2018

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Characterization of the P140K, PVP(138-140)MLK, and G156A O6-methylguanine-DNA methyltransferase mutants: implications for drug resistance gene therapy

21 January 2018

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Methylguanine methyltransferase-mediated in vivo selection and chemoprotection of allogeneic stem cells in a large-animal model

21 January 2018

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In vivo selection of MGMT(P140K) lentivirus–transduced human NOD/SCID repopulating cells without pretransplant irradiation conditioning

21 January 2018

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In vivo selection of human hematopoietic cells in a xenograft model using combined pharmacologic and genetic manipulations

21 January 2018

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Successful treatment of murine beta-thalassemia using in vivo selection of genetically modified, drug-resistant hematopoietic stem cells

21 January 2018

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Erythropoietic protoporphyria in the house mouse. A recessive inherited ferrochelatase deficiency with anemia, photosensitivity, and liver disease

21 January 2018

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Successful therapeutic effect in a mouse model of erythropoietic protoporphyria by partial genetic correction and fluorescence-based selection of hematopoietic cells

21 January 2018

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Long-term cure of the photosensitivity of murine erythropoietic protoporphyria by preselective gene therapy

21 January 2018

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Gene therapy of a mouse model of protoporphyria with a self-inactivating erythroid-specific lentiviral vector without preselection.

21 January 2018

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A bicistronic SIN-lentiviral vector containing G156A MGMT allows selection and metabolic correction of hematopoietic protoporphyric cell lines

21 January 2018

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Retroviral transfer and long-term expression of the adrenoleukodystrophy gene in human CD34+ cells

21 January 2018

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https://api.crossref.org/works/10.1038%2FSJ.GT.3302335

Prolonged production of NADPH oxidase-corrected granulocytes after gene therapy of chronic granulomatous disease

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302335

In vivo selection for human and murine hematopoietic cells transduced with a therapeutic MGMT lentiviral vector that inhibits HIV replication

21 January 2018

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https://api.crossref.org/works/10.1038%2FSJ.GT.3302335

Myeloablation enhances engraftment of transduced murine hematopoietic cells, but does not influence long-term expression of the transgene

21 January 2018

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https://api.crossref.org/works/10.1038%2FSJ.GT.3302335

Enhanced antitumor activity of sarCNU in comparison to BCNU in an extraneuronal monoamine transporter positive human glioma xenograft model

21 January 2018

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https://api.crossref.org/works/10.1038%2FSJ.GT.3302335

SarCNU mediates selection of P140K methylguanine-DNA-methyltransferase transduced human CD34(+) cells in vitro.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302335

Protection and in vivo selection of hematopoietic stem cells using temozolomide, O6-benzylguanine, and an alkyltransferase-expressing retroviral vector

21 January 2018

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https://api.crossref.org/works/10.1038%2FSJ.GT.3302335

High-level erythroid-specific gene expression in primary human and murine hematopoietic cells with self-inactivating lentiviral vectors

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302335

Enhanced transgene expression in cord blood CD34(+)-derived hematopoietic cells, including developing T cells and NOD/SCID mouse repopulating cells, following transduction with modified trip lentiviral vectors

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302335

7 January 2021

Development of a self-inactivating lentivirus vector.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302335

7 January 2021

Prolonged high-level detection of retrovirally marked hematopoietic cells in nonhuman primates after transduction of CD34+ progenitors using clinically feasible methods

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302335

7 January 2021

The penetrance of dominant erythropoietic protoporphyria is modulated by expression of wildtype FECH

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302335

7 January 2021

A simple ferrochelatase assay

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302335

7 January 2021

Identifiers

DOI

10.1038/SJ.GT.3302335

1 reference

Dimensions Publication ID

8 December 2017

1035675180

0 references

1 reference