(Q45129138)
Statements
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Transgenic mouse expressing human mutant alpha-galactosidase A in an endogenous enzyme deficient background: a biochemical animal model for studying active-site specific chaperone therapy for Fabry disease (English)
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Satoshi Ishii
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Hidekatsu Yoshioka
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Kazuaki Mannen
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Ashok B Kulkarni
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Jian-Qiang Fan
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1 November 2004
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