(Q45361267)

13 December 2017

Long-term functional adeno-associated virus-microdystrophin expression in the dystrophic CXMDj dog. (English)

1 reference

13 December 2017

Taeyoung Koo

1

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13 December 2017

Takashi Okada

2

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13 December 2017

Takis Athanasopoulos

3

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13 December 2017

Helen Foster

4

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13 December 2017

Shin'ichi Takeda

5

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13 December 2017

George Dickson

6

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13 December 2017

1 September 2011

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13 December 2017

Journal of Gene Medicine

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13 December 2017

13

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13 December 2017

9

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13 December 2017

497-506

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Dystrophin and mutations: one gene, several proteins, multiple phenotypes

13 December 2017

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Muscle damage in mdx (dystrophic) mice: role of calcium and reactive oxygen species.

21 January 2018

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Systemic microdystrophin gene delivery improves skeletal muscle structure and function in old dystrophic mdx mice.

21 January 2018

1 reference

Adeno-associated virus vector gene transfer and sarcolemmal expression of a 144 kDa micro-dystrophin effectively restores the dystrophin-associated protein complex and inhibits myofibre degeneration in nude/mdx mice

21 January 2018

1 reference

Recombinant adeno-associated viral (rAAV) vectors as therapeutic tools for Duchenne muscular dystrophy (DMD).

21 January 2018

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Dystrophins carrying spectrin-like repeats 16 and 17 anchor nNOS to the sarcolemma and enhance exercise performance in a mouse model of muscular dystrophy.

21 January 2018

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Effect of genome size on AAV vector packaging

21 January 2018

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Immunity to adeno-associated virus-mediated gene transfer in a random-bred canine model of Duchenne muscular dystrophy

21 January 2018

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Injection of a recombinant AAV serotype 2 into canine skeletal muscles evokes strong immune responses against transgene products

21 January 2018

1 reference

AAV vector-mediated microdystrophin expression in a relatively small percentage of mdx myofibers improved the mdx phenotype

21 January 2018

1 reference

Transduction efficiency and immune response associated with the administration of AAV8 vector into dog skeletal muscle

21 January 2018

1 reference

Expression of dog microdystrophin in mouse and dog muscles by gene therapy

21 January 2018

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Efficient transduction of skeletal muscle using vectors based on adeno-associated virus serotype 6.

21 January 2018

1 reference

Long-term expression and repeated administration of AAV type 1, 2 and 5 vectors in skeletal muscle of immunocompetent adult mice

21 January 2018

1 reference

Dystrophin immunity in Duchenne's muscular dystrophy.

21 January 2018

1 reference

Synthetic muscle promoters: activities exceeding naturally occurring regulatory sequences

21 January 2018

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Large-scale production of recombinant viruses by use of a large culture vessel with active gassing

21 January 2018

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Scalable purification of adeno-associated virus serotype 1 (AAV1) and AAV8 vectors, using dual ion-exchange adsorptive membranes.

21 January 2018

1 reference

Ultraconserved Elements in the Human Genome

21 January 2018

1 reference

Function and genetics of dystrophin and dystrophin-related proteins in muscle

21 January 2018

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Three muscular dystrophies: loss of cytoskeleton-extracellular matrix linkage.

21 January 2018

1 reference

Increasing complexity of the dystrophin-associated protein complex

21 January 2018

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Assembly of the dystrophin-associated protein complex does not require the dystrophin COOH-terminal domain

21 January 2018

1 reference

Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response

21 January 2018

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Widespread muscle expression of an AAV9 human mini-dystrophin vector after intravenous injection in neonatal dystrophin-deficient dogs

21 January 2018

1 reference

Dystrophin levels as low as 30% are sufficient to avoid muscular dystrophy in the human

21 January 2018

1 reference

21 January 2018

Identifiers

DOI

10.1002/JGM.1602

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13 December 2017

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