(Q45711198)

15 December 2017

Adeno-associated virus vector-mediated transduction in the cat brain (English)

1 reference

15 December 2017

0 references

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A14502216

12 March 2024

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302087

12 March 2024

1 reference

https://api.crossref.org/works/10.1038/SJ.GT.3302087

12 March 2024

author name string

Charles H. Vite

1

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A14502216

12 March 2024

Marco A. Passini

2

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A14502216

12 March 2024

Mark E. Haskins

3

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A14502216

12 March 2024

John H. Wolfe

4

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A14502216

12 March 2024

language of work or name

1 reference

1 October 2003

1 reference

full work available at URL

15 December 2017

https://www.nature.com/articles/3302087.pdf

file format

Portable Document Format

online access status

open access

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A14502216

https://www.nature.com/articles/3302087.pdf

12 March 2024

file format

Portable Document Format

1 reference

DOI

https://api.crossref.org/works/10.1038/SJ.GT.3302087

https://www.nature.com/articles/3302087

12 March 2024

1 reference

DOI

https://api.crossref.org/works/10.1038/SJ.GT.3302087

12 March 2024

1 reference

15 December 2017

10

1 reference

15 December 2017

22

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15 December 2017

1874-1881

1 reference

https://scigraph.springernature.com/pub.10.1038/sj.gt.3302087

15 December 2017

0 references

cites work

Brain-directed gene therapy for lysosomal storage disease: going well beyond the blood- brain barrier

1 reference

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Sustained production of beta-glucuronidase from localized sites after AAV vector gene transfer results in widespread distribution of enzyme and reversal of lysosomal storage lesions in a large volume of brain in mucopolysaccharidosis VII mice.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

Neonatal gene transfer leads to widespread correction of pathology in a murine model of lysosomal storage disease.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

Elimination of lysosomal storage in brains of MPS VII mice treated by intrathecal administration of an adeno-associated virus vector

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

Reversal of pathology in the entire brain of mucopolysaccharidosis type VII mice after lentivirus-mediated gene transfer.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

Widespread gene delivery and structure-specific patterns of expression in the brain after intraventricular injections of neonatal mice with an adeno-associated virus vector

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

Functional correction of established central nervous system deficits in an animal model of lysosomal storage disease with feline immunodeficiency virus-based vectors

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

Lysosomal storage diseases of animals: an essay in comparative pathology

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

Building a better vector: the manipulation of AAV virions

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

Recombinant adeno-associated virus type 2, 4, and 5 vectors: transduction of variant cell types and regions in the mammalian central nervous system.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

Herpesvirus vector gene transfer and expression of beta-glucuronidase in the central nervous system of MPS VII mice

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

Decreased lysosomal storage in the adult MPS VII mouse brain in the vicinity of grafts of retroviral vector-corrected fibroblasts secreting high levels of beta-glucuronidase

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

Enhancement of muscle gene delivery with pseudotyped adeno-associated virus type 5 correlates with myoblast differentiation.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

Cross-packaging of a single adeno-associated virus (AAV) type 2 vector genome into multiple AAV serotypes enables transduction with broad specificity

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

Binding of adeno-associated virus type 5 to 2,3-linked sialic acid is required for gene transfer

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

Recombinant adeno-associated virus-mediated correction of lysosomal storage within the central nervous system of the adult mucopolysaccharidosis type VII mouse

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

Enhanced secretion and uptake of beta-glucuronidase improves adeno-associated viral-mediated gene therapy of mucopolysaccharidosis type VII mice

21 January 2018

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https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

Intracranial injection of recombinant adeno-associated virus improves cognitive function in a murine model of mucopolysaccharidosis type VII.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

Neurological correction of lysosomal storage in a mucopolysaccharidosis IIIB mouse model by adeno-associated virus-mediated gene delivery

21 January 2018

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Long-term gene expression and phenotypic correction using adeno-associated virus vectors in the mammalian brain

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

Differential and persistent expression patterns of CNS gene transfer by an adeno-associated virus (AAV) vector

21 January 2018

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In vivo expression of therapeutic human genes for dopamine production in the caudates of MPTP-treated monkeys using an AAV vector

21 January 2018

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https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

Adeno-associated virus vectors: activity and applications in the CNS.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

Adeno-associated virus vector-mediated bcl-2 gene transfer into post-ischemic gerbil brain in vivo: prospects for gene therapy of ischemia-induced neuronal death

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

Recombinant adeno-associated virus serotypes 2- and 5-mediated gene transfer in the mammalian brain: quantitative analysis of heparin co-infusion

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

Selective and rapid uptake of adeno-associated virus type 2 in brain

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

Hybrid vectors based on adeno-associated virus serotypes 2 and 5 for muscle-directed gene transfer

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

Selective neurodegeneration in murine mucopolysaccharidosis VII is progressive and reversible.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

In utero transplantation of fetal liver cells in the mucopolysaccharidosis type VII mouse results in low-level chimerism, but overexpression of beta-glucuronidase can delay onset of clinical signs

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

7 January 2021

Hurler and Hunter syndromes: mutual correction of the defect in cultured fibroblasts

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

7 January 2021

Infectious clones and vectors derived from adeno-associated virus (AAV) serotypes other than AAV type 2.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

7 January 2021

Membrane-associated heparan sulfate proteoglycan is a receptor for adeno-associated virus type 2 virions

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

7 January 2021

Distribution of a lysosomal enzyme in the adult brain by axonal transport and by cells of the rostral migratory stream.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

7 January 2021

In situ hybridization studies of retinal neurons

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302087

7 January 2021

Identifiers

DOI

1 reference

Dimensions Publication ID

15 December 2017

0 references

1 reference