(Q45856667)
Statements
AAV8-mediated expression of glucocerebrosidase ameliorates the storage pathology in the visceral organs of a mouse model of Gaucher disease (English)
Kerry Anne McEachern
Jennifer B Nietupski
Wei-Lien Chuang
Donna Armentano
Jennifer Johnson
Elizabeth Hutto
Gregory A Grabowski
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1 reference
1 reference