(Q45859200)
Statements
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Gene therapy for canine alpha-L-iduronidase deficiency: in utero adoptive transfer of genetically corrected hematopoietic progenitors results in engraftment but not amelioration of disease (English)
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Lutzko C
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Omori F
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Abrams-Ogg AC
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Shull R
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Li L
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Lau K
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Ruedy C
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Nanji S
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Gartley C
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Dobson H
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Foster R
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Kruth S
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Dubé ID
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1 June 1999
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10
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9
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1521-1532
1 reference