(Q45865415)
Statements
Lentiviral vectors containing a retinal pigment epithelium specific promoter for leber congenital amaurosis gene therapy. Lentiviral gene therapy for LCA (English)
Dana Hornfeld
Muriel Jaquet
William W Hauswirth
Janis Lem
Zhongyan Wang
Daniel E Schorderet
Francis L Munier
Andreas Wenzel
Yvan Arsenijevic