(Q45873416)
Statements
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Gene transfer of low levels of beta-glucuronidase corrects hepatic lysosomal storage in a large animal model of mucopolysaccharidosis VII. (English)
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Wolfe JH
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Sands MS
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Harel N
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Weil MA
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Parente MK
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Polesky AC
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Reilly JJ
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Hasson C
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Weimelt S
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Haskins ME
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1 December 2000
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2
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6
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552-561
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Identifiers
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