(Q45875559)

17 December 2017

title

Transgenic rescue of Krabbe disease in the twitcher mouse (English)

1 reference

17 December 2017

1 reference

De Gasperi R

1

1 reference

17 December 2017

Friedrich VL

2

1 reference

17 December 2017

Perez GM

3

1 reference

17 December 2017

Senturk E

4

1 reference

17 December 2017

Wen PH

5

1 reference

17 December 2017

Kelley K

6

1 reference

17 December 2017

Elder GA

7

1 reference

17 December 2017

Gama Sosa MA

8

1 reference

17 December 2017

publication date

1 August 2004

1 reference

17 December 2017

published in

Gene Therapy

1 reference

17 December 2017

volume

11

1 reference

17 December 2017

issue

15

1 reference

17 December 2017

page(s)

1188-1194

1 reference

17 December 2017

https://scigraph.springernature.com/pub.10.1038/sj.gt.3302282

exact match

0 references

cites work

Twenty five years of the "psychosine hypothesis": a personal perspective of its history and present status

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302282

Murine model of genetic demyelinating disease: the twitcher mouse

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302282

Hematopoietic cell transplantation in murine globoid cell leukodystrophy (the twitcher mouse): effects on levels of galactosylceramidase, psychosine, and galactocerebrosides

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302282

Donor-derived cells in the central nervous system of twitcher mice after bone marrow transplantation

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302282

Effect of bone marrow transplantation on enzyme levels and clinical course in the neurologically affected twitcher mouse

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302282

Hematopoietic cell transplantation after administration of high-dose busulfan in murine globoid cell leukodystrophy (the twitcher mouse).

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302282

Prolonged survival and remyelination after hematopoietic cell transplantation in the twitcher mouse.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302282

Correction of the galactocerebrosidase deficiency in globoid cell leukodystrophy-cultured cells by SL3-3 retroviral-mediated gene transfer

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302282

Transduction of cultured oligodendrocytes from normal and twitcher mice by a retroviral vector containing human galactocerebrosidase (GALC) cDNA.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302282

Retroviral-mediated transfer of the galactocerebrosidase gene in neural progenitor cells

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302282

Retroviral vector-mediated transfer of the galactocerebrosidase (GALC) cDNA leads to overexpression and transfer of GALC activity to neighboring cells

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302282

Intraventricular administration of recombinant adenovirus to neonatal twitcher mouse leads to clinicopathological improvements

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302282

The twitcher mouse: a model for Krabbe disease and for experimental therapies

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302282

Expression and processing of recombinant human galactosylceramidase

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302282

Structure and organization of the human galactocerebrosidase (GALC) gene

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302282

Molecular cloning and expression of cDNA for murine galactocerebrosidase and mutation analysis of the twitcher mouse, a model of Krabbe's disease

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302282

Isolation of biologically active ribonucleic acid from sources enriched in ribonuclease

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302282

Cloning and expression of cDNA encoding human galactocerebrosidase, the enzyme deficient in globoid cell leukodystrophy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302282

Hematopoietic cell transplantation in the twitcher mouse. The effects of pretransplant conditioning with graded doses of busulfan.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302282

7 January 2021

An accumulation of galactocerebroside in kidney from mouse globoid cell leukodystrophy (twitcher)

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302282

7 January 2021

Abnormal accumulation of galactosylceramide in the kidney of twitcher mouse

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302282

7 January 2021

BAC and PAC DNA for the generation of transgenic animals.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302282

7 January 2021

Identifiers

DOI

10.1038/SJ.GT.3302282

1 reference

17 December 2017

Dimensions Publication ID

1028028782

0 references

1 reference

17 December 2017