(Q45876060)
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In vivo genome editing using nuclease-encoding mRNA corrects SP-B deficiency (English)
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Azita J Mahiny
Alexander Dewerth
Lauren E Mays
Mohammed Alkhaled
Benedikt Mothes
Emad Malaeksefat
Jennifer Rottenberger
Darina M Brosch
Philipp Reautschnig
Pacharapan Surapolchai
Franziska Zeyer
Andrea Schams
Melanie Carevic
Martina Bakele
Matthias Griese
Matthias Schwab
Sandra Beer-Hammer
Rupert Handgretinger
Dominik Hartl
Michael S D Kormann
Claus-Michael Lehr
18 May 2015
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