(Q45882531)
Statements
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Gene therapy for lysosomal storage disease: a no-brainer? Transplants of fibroblasts secreting high levels of beta-glucuronidase decrease lesions in the brains of mice with Sly syndrome, a lysosomal storage disease (English)
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Sly WS
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Vogler C
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1 July 1997
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3
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7
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719-720
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Identifiers
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