(Q46272554)
Statements
1 reference
Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy (English)
1 reference
Richard S Finkel
Anne M Connolly
Nancy L Kuntz
Claudia A Chiriboga
Kayoko Saito
Eduardo Tizzano
Már Tulinius
Jacqueline Montes
Allan M Glanzman
Kathie Bishop
Z John Zhong
Sarah Gheuens
C Frank Bennett
Eugene Schneider
Wildon Farwell
Darryl C De Vivo
ENDEAR Study Group
1 November 2017
1 reference