(Q51891201)
Statements
Outcome in six children with mucopolysaccharidosis type IH, Hurler syndrome, after haematopoietic stem cell transplantation (HSCT). (English)
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Gunilla Malm
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Britt Gustafsson
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Gunilla Berglund
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Maria Lindström
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Karin Naess
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Birgit Borgström
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Ulrika von Döbeln
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Olle Ringdén
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29 April 2008
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97
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8
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1108-1112
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