(Q58923973)
Statements
In vitro restoration of functional SMN protein in human trophoblast cells affected by spinal muscular atrophy by small fragment homologous replacement (English)
Antonio Filareto
Paola Spitalieri
Maria Lucia Scaldaferri
Ruggiero Mango
Emanuela Bruscia
Gennaro Citro
Ercole Brunetti