(Q63560628)
Statements
In vivo transduction by intravenous injection of a lentiviral vector expressing human ADA into neonatal ADA gene knockout mice: a novel form of enzyme replacement therapy for ADA deficiency (English)
Xiangyang Jin
Denise Petersen
Xingchao Wang
Fred Dorey
Ki Soo Kil
Melissa Aldrich
Denise A Carbonaro
Rodney E Kellems
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