(Q80501077)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:17579573%20AND%20SRC:MED&resulttype=core&format=json

1 January 2020

title

Morpholino oligomer-mediated exon skipping averts the onset of dystrophic pathology in the mdx mouse (English)

1 reference

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1 January 2020

1 reference

1

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1 January 2020

Patrick L Iversen

8

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1 January 2020

author name string

Kaite Honeyman

2

1 reference

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1 January 2020

Abbie M Fall

3

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1 January 2020

Penny L Harding

4

1 reference

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1 January 2020

Russell D Johnsen

5

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1 January 2020

Joshua P Steinhaus

6

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1 January 2020

Hong M Moulton

7

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1 January 2020

Stephen D Wilton

9

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1 January 2020

publication date

19 June 2007

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1 January 2020

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1 January 2020

volume

15

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1 January 2020

issue

9

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1 January 2020

page(s)

1587-1592

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RNA splicing manipulation: strategies to modify gene expression for a variety of therapeutic outcomes.

1 January 2020

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7 January 2021

Antisense oligonucleotides in the treatment of Duchenne muscular dystrophy: Where are we now?

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7 January 2021

Gene therapy: the 'pro-sense' approach to Duchenne muscular dystrophy

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Muscular dystrophy into the new millennium

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Dystrophin and mutations: one gene, several proteins, multiple phenotypes

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7 January 2021

Novel dystrophin mutations revealed by analysis of dystrophin mRNA: alternative splicing suppresses the phenotypic effect of a nonsense mutation

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7 January 2021

Searching for the 1 in 2,400,000: a review of dystrophin gene point mutations

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7 January 2021

An explanation for the phenotypic differences between patients bearing partial deletions of the DMD locus

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7 January 2021

Clinical variability in Becker muscular dystrophy. Genetic, biochemical and immunohistochemical correlates

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7 January 2021

Very mild muscular dystrophy associated with the deletion of 46% of dystrophin

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7 January 2021

Effect of dystrophin gene deletions on mRNA levels and processing in Duchenne and Becker muscular dystrophies

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7 January 2021

Giant dystrophin deletion associated with congenital cataract and mild muscular dystrophy.

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7 January 2021

Massive idiosyncratic exon skipping corrects the nonsense mutation in dystrophic mouse muscle and produces functional revertant fibers by clonal expansion

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7 January 2021

Revertant fibres: a possible genetic therapy for Duchenne muscular dystrophy?

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7 January 2021

Immunohistological evidence for second or somatic mutations as the underlying cause of dystrophin expression by isolated fibres in Xp21 muscular dystrophy of Duchenne-type severity

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7 January 2021

Comparative analysis of antisense oligonucleotide analogs for targeted DMD exon 46 skipping in muscle cells

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7 January 2021

Dystrophin expression in the mdx mouse after localised and systemic administration of a morpholino antisense oligonucleotide

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7 January 2021

Terminal antisense oligonucleotide modifications can enhance induced exon skipping

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7 January 2021

Morpholino antisense oligonucleotide induced dystrophin exon 23 skipping in mdx mouse muscle.

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7 January 2021

Stability of cell-penetrating peptide-morpholino oligomer conjugates in human serum and in cells.

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7 January 2021

Systemic delivery of morpholino oligonucleotide restores dystrophin expression bodywide and improves dystrophic pathology

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7 January 2021

Improved antisense oligonucleotide induced exon skipping in the mdx mouse model of muscular dystrophy

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7 January 2021

Therapeutics for Duchenne muscular dystrophy: current approaches and future directions.

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7 January 2021

Duchenne muscular dystrophy: current knowledge, treatment, and future prospects.

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7 January 2021

Steroids in Duchenne muscular dystrophy: from clinical trials to genomic research

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7 January 2021

Survival in Duchenne muscular dystrophy: improvements in life expectancy since 1967 and the impact of home nocturnal ventilation

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7 January 2021

Antisense-induced multiexon skipping for Duchenne muscular dystrophy makes more sense

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7 January 2021

Therapeutic antisense-induced exon skipping in cultured muscle cells from six different DMD patients.

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7 January 2021

Functional amounts of dystrophin produced by skipping the mutated exon in the mdx dystrophic mouse

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7 January 2021

Systemic delivery of antisense oligoribonucleotide restores dystrophin expression in body-wide skeletal muscles

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7 January 2021

Morpholino antisense oligomers: the case for an RNase H-independent structural type

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7 January 2021

Muscular weakness in the mdx mouse

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7 January 2021

Antisense-induced exon skipping restores dystrophin expression in DMD patient derived muscle cells

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7 January 2021

Induced dystrophin exon skipping in human muscle explants

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7 January 2021

Rescue of dystrophic muscle through U7 snRNA-mediated exon skipping

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7 January 2021

Vectorization of morpholino oligomers by the (R-Ahx-R)4 peptide allows efficient splicing correction in the absence of endosomolytic agents.

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7 January 2021

Antisense oligonucleotide-induced exon skipping restores dystrophin expression in vitro in a canine model of DMD.

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7 January 2021

X chromosome-linked muscular dystrophy (mdx) in the mouse

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7 January 2021

The molecular basis of muscular dystrophy in the mdx mouse: a point mutation

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7 January 2021

Identifiers

DOI

10.1038/SJ.MT.6300245

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:17579573%20AND%20SRC:MED&resulttype=core&format=json

1 January 2020

1 reference