(Q80820588)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:15464431%20AND%20SRC:MED&resulttype=core&format=json

3 January 2020

title

Intrathecal enzyme replacement therapy reduces lysosomal storage in the brain and meninges of the canine model of MPS I (English)

1 reference

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3 January 2020

2

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3 January 2020

author name string

Kakkis E

1

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3 January 2020

Vogler C

3

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3 January 2020

Le S

4

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3 January 2020

Levy B

5

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3 January 2020

Belichenko P

6

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3 January 2020

Mobley W

7

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3 January 2020

Dickson P

8

1 reference

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3 January 2020

Hanson S

9

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3 January 2020

Passage M

10

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3 January 2020

publication date

1 September 2004

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:15464431%20AND%20SRC:MED&resulttype=core&format=json

Molecular Genetics and Metabolism

3 January 2020

published in

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3 January 2020

volume

83

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3 January 2020

issue

1-2

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3 January 2020

page(s)

163-174

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Cervical cord compression in mucopolysaccharidosis

3 January 2020

cites work

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMGME.2004.07.003

Spinal pachymeningitis secondary to mucopolysaccharidosis. Case report.

7 January 2021

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Myelography Features of Mucopolysaccharidoses: A New Sign

7 January 2021

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Cervical myelopathy due to dural compression in mucopolysaccharidosis

7 January 2021

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Computed tomography studies on patients with mucopolysaccharidoses

7 January 2021

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Reversal of clinical features of Hurler's disease and biochemical improvement after treatment by bone-marrow transplantation

7 January 2021

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Bone marrow transplantation for mucopolysaccharidosis type I: experience of two British centres

7 January 2021

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Long-term outcome of Hurler syndrome following bone marrow transplantation.

7 January 2021

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Long-term clinical progress in bone marrow transplanted mucopolysaccharidosis type I patients with a defined genotype

7 January 2021

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Allogeneic bone marrow transplantation for lysosomal storage diseases. The European Group for Bone Marrow Transplantation

7 January 2021

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Replacement therapy for inherited enzyme deficiency--macrophage-targeted glucocerebrosidase for Gaucher's disease

7 January 2021

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Enzyme replacement therapy for mucopolysaccharidosis I: a randomized, double-blinded, placebo-controlled, multinational study of recombinant human alpha-L-iduronidase (laronidase).

7 January 2021

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Safety and efficacy of recombinant human alpha-galactosidase A replacement therapy in Fabry's disease

7 January 2021

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Enzyme replacement therapy in Fabry disease: a randomized controlled trial

7 January 2021

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Enzyme-replacement therapy in mucopolysaccharidosis I.

7 January 2021

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Outwitting the blood-brain barrier for therapeutic purposes: osmotic opening and other means

7 January 2021

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Drug delivery to the brain

7 January 2021

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New advances in the transport of doxorubicin through the blood-brain barrier by a peptide vector-mediated strategy.

7 January 2021

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High transcytosis of melanotransferrin (P97) across the blood-brain barrier

7 January 2021

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Delivery, distribution, and neuronal uptake of exogenous mannose-terminal glucocerebrosidase in the intact rat brain.

7 January 2021

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Convection-enhanced delivery of macromolecules in the brain

7 January 2021

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Heparin coinfusion during convection-enhanced delivery (CED) increases the distribution of the glial-derived neurotrophic factor (GDNF) ligand family in rat striatum and enhances the pharmacological activity of neurturin

7 January 2021

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Tumor regression with regional distribution of the targeted toxin TF-CRM107 in patients with malignant brain tumors.

7 January 2021

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Long-term and high-dose trials of enzyme replacement therapy in the canine model of mucopolysaccharidosis I.

7 January 2021

1 reference

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Overexpression of the human lysosomal enzyme alpha-L-iduronidase in Chinese hamster ovary cells

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMGME.2004.07.003

Immune tolerance after long-term enzyme-replacement therapy among patients who have mucopolysaccharidosis I

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMGME.2004.07.003

Uptake of alpha-(L)-iduronidase produced by retrovirally transduced fibroblasts into neuronal and glial cells in vitro

7 January 2021

1 reference

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Uptake of recombinant iduronate-2-sulfatase into neuronal and glial cells in vitro.

7 January 2021

1 reference

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Uptake of mannose-terminal glucocerebrosidase in cultured human cholinergic and dopaminergic neuron cell lines.

7 January 2021

1 reference

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Aspartylglucosaminidase (AGA) is efficiently produced and endocytosed by glial cells: implication for the therapy of a lysosomal storage disorder

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMGME.2004.07.003

The increased sensitivity of neurons with elevated glucocerebroside to neurotoxic agents can be reversed by imiglucerase

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMGME.2004.07.003

10.1016/J.YMGME.2004.07.003

7 January 2021

Identifiers

DOI

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:15464431%20AND%20SRC:MED&resulttype=core&format=json

3 January 2020

1 reference