(Q85263690)
Statements
Efficacy of 2-Hydroxypropyl-β-cyclodextrin in Niemann-Pick Disease Type C Model Mice and Its Pharmacokinetic Analysis in a Patient with the Disease (English)
Yuta Tanaka
Muneaki Matsuo
Koki Shiraishi
Koki Wada
Yushiro Uchio
Yuki Kondo
Toru Takeo
Naomi Nakagata
Taishi Higashi
Keiichi Motoyama
Hidetoshi Arima
Sakiko Mochinaga
Katsumi Higaki
Kousaku Ohno
Tetsumi Irie
1 January 2015