(Q28277595)

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Recombinant human acid [alpha]-glucosidase: major clinical benefits in infantile-onset Pompe disease

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Recombinant human acid [alpha]-glucosidase: major clinical benefits in infantile-onset Pompe disease (English)
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P S Kishnani
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D Corzo
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M Nicolino
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B Byrne
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H Mandel
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N Leslie
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J Levine
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C Spencer
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M McDonald
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J Li
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J Dumontier
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M Halberthal
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Y H Chien
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S Vijayaraghavan
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D Gruskin
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D Bartholomew
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A van der Ploeg
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J P Clancy
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R Parini
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G Morin
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M Beck
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G S De la Gastine
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M Jokic
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S Richards
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D Bali
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M Davison
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M A Worden
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Y T Chen
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J E Wraith
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9 January 2007
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68
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2
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99-109
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